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論文リスト

doi title author source_title year
191 10.1001/jamaoncol.2017.4695 Differentiation Syndrome Associated With Enasidenib, A Selective Inhibitor Of Mutant Isocitrate Dehydrogenase 2 Fathi, Amir T.; Dinardo, Courtney D.; Kline, Irina; Kenvin, Laurie; Gupta, Ira; Attar, Eyal C.; Stein, Eytan M.; De Botton, Stephane Jama Oncology 2018
1315 10.1002/ajh.25638 Munir, Talha, 0000-0002-2901-0769; Brown, Jennifer R.; O’Brien, Susan, 0000-0002-2481-7504; Barrientos, Jacqueline C.; Barr, Paul M.; Reddy, Nishitha M.; Coutre, Steven; Tam, Constantine S.; Mulligan, Stephen P.; Jaeger, Ulrich; Kipps, Thomas J.; Moreno, Carol, 0000-0003-3275-0271; Montillo, Marco; Burger, Jan A.; Byrd, John C.; Hillmen, Peter; Dai, Sandra; Szoke, Anita; Dean, James P.; Woyach, Jennifer A. American Journal Of Hematology 2019
2672 10.1007/s11032-019-0954-y Enhanced Rice Salinity Tolerance Via Crispr/Cas9-Targeted Mutagenesis Of The Osrr22 Gene Zhang, Anning; Liu, Yi; Wang, Feiming; Li, Tianfei; Chen, Zhihao; Kong, Deyan; Bi, Junguo; Zhang, Fenyun; Luo, Xingxing; Wang, Jiahong; Tang, Jinjuan; Yu, Xinqiao; Liu, Guolan; Luo, Lijun Molecular Breeding 2019
3150 10.1016/j.annonc.2020.09.019 Chronic Lymphocytic Leukaemia: Esmo Clinical Practice Guidelines For Diagnosis, Treatment And Follow-Up Eichhorst, B.; Robak, T.; Montserrat, E.; Ghia, P.; Niemann, C.U.; Kater, A.P.; Gregor, M.; Cymbalista, F.; Buske, C.; Hillmen, P.; Hallek, M.; Mey, U. Annals Of Oncology 2021
3896 10.1016/j.ccell.2018.10.005 Inhibition Of Amino Acid Metabolism Selectively Targets Human Leukemia Stem Cells Jones, Courtney L.; Stevens, Brett M.; D’Alessandro, Angelo; Reisz, Julie A.; Culp-Hill, Rachel; Nemkov, Travis; Pei, Shanshan; Khan, Nabilah; Adane, Biniam; Ye, Haobin; Krug, Anna; Reinhold, Dominik; Smith, Clayton; Degregori, James; Pollyea, Daniel A.; Jordan, Craig T. Cancer Cell 2018
3905 10.1016/j.ccell.2019.06.003 Mubritinib Targets The Electron Transport Chain Complex I And Reveals The Landscape Of Oxphos Dependency In Acute Myeloid Leukemia Baccelli, Irene; Gareau, Yves; Lehnertz, Bernhard; Gingras, Stephane; Spinella, Jean-Francois; Corneau, Sophie; Mayotte, Nadine; Girard, Simon; Frechette, Melanie; Blouin-Chagnon, Valerie; Leveille, Koryne; Boivin, Isabel; Macrae, Tara; Krosl, Jana; Thiollier, Clarisse; Lavallee, Vincent-Philippe; Kanshin, Evgeny; Bertomeu, Thierry; Coulombe-Huntington, Jasmin; St-Denis, Corinne; Bordeleau, Marie-Eve; Boucher, Genevieve; Roux, Philippe P.; Lemieux, Sebastien; Tyers, Mike; Thibault, Pierre; Hebert, Josee; Marinier, Anne; Sauvageau, Guy Cancer Cell 2019
3906 10.1016/j.ccell.2019.08.005 Mitochondrial Reprogramming Underlies Resistance To Bcl-2 Inhibition In Lymphoid Malignancies Guieze, Romain; Liu, Vivian M.; Rosebrock, Daniel; Jourdain, Alexis A.; Hernandez-Sanchez, Maria; Martinez Zurita, Aina; Sun, Jing; Ten Hacken, Elisa; Baranowski, Kaitlyn; Thompson, Philip A.; Heo, Jin-Mi; Cartun, Zachary; Aygun, Ozan; Iorgulescu, J. Bryan; Zhang, Wandi; Notarangelo, Giulia; Livitz, Dimitri; Li, Shuqiang; Davids, Matthew S.; Biran, Anat; Fernandes, Stacey M.; Brown, Jennifer R.; Lako, Ana; Ciantra, Zoe B.; Lawlor, Matthew A.; Keskin, Derin B.; Udeshi, Namrata D.; Wierda, William G.; Livak, Kenneth J.; Letai, Anthony G.; Neuberg, Donna; Harper, J. Wade; Carr, Steven A.; Piccioni, Federica; Ott, Christopher J.; Leshchiner, Ignaty; Johannessen, Cory M.; Doench, John; Mootha, Vamsi K.; Getz, Gad; Wu, Catherine J. Cancer Cell 2019
4376 10.1016/j.cell.2020.05.037 Determinants Of Base Editing Outcomes From Target Library Analysis And Machine Learning Arbab, Mandana; Shen, Max W.; Mok, Beverly; Wilson, Christopher; Matuszek, <U+017B>aneta; Cassa, Christopher A.; Liu, David R., 0000-0002-9943-7557 Cell 2020
6828 10.1016/j.jacc.2019.07.056 Cardiovascular Toxicities Associated With Ibrutinib Salem, Joe-Elie; Manouchehri, Ali; Bretagne, Marie; Lebrun-Vignes, Benedicte; Groarke, John D.; Johnson, Douglas B.; Yang, Tao; Reddy, Nishitha M.; Funck-Brentano, Christian; Brown, Jennifer R.; Roden, Dan M.; Moslehi, Javid J. Journal Of The American College Of Cardiology 2019
6863 10.1016/j.jaci.2018.08.024 Consensus Approach For The Management Of Severe Combined Immune Deficiency Caused By Adenosine Deaminase Deficiency Kohn, Donald B.; Hershfield, Michael S.; Puck, Jennifer M.; Aiuti, Alessandro; Blincoe, Annaliesse; Gaspar, H. Bobby; Notarangelo, Luigi D.; Grunebaum, Eyal Journal Of Allergy And Clinical Immunology 2019
8207 10.1016/j.molcel.2018.12.003 A Compact, High-Accuracy Cas9 With A Dinucleotide Pam For In Vivo Genome Editing Edraki, Alireza; Mir, Aamir; Ibraheim, Raed; Gainetdinov, Ildar; Yoon, Yeonsoo; Song, Chun-Qing; Cao, Yueying; Gallant, Judith; Xue, Wen; Rivera-Perez, Jaime A.; Sontheimer, Erik J. Molecular Cell 2019
8331 10.1016/j.molp.2019.03.009 Genome Engineering In Rice Using Cas9 Variants That Recognize Ng Pam Sequences Hua, Kai; Tao, Xiaoping; Han, Peijin; Wang, Rui; Zhu, Jian-Kang Molecular Plant 2019
8332 10.1016/j.molp.2019.03.010 Cas9-Ng Greatly Expands The Targeting Scope Of The Genome-Editing Toolkit By Recognizing Ng And Other Atypical Pams In Rice Ren, Bin; Liu, Lang; Li, Shaofang; Kuang, Yongjie; Wang, Jingwen; Zhang, Dawei; Zhou, Xueping; Lin, Honghui; Zhou, Huanbin Molecular Plant 2019
8333 10.1016/j.molp.2019.03.011 Improving Plant Genome Editing With High-Fidelity Xcas9 And Non-Canonical Pam-Targeting Cas9-Ng Zhong, Zhaohui; Sretenovic, Simon; Ren, Qiurong; Yang, Lijia; Bao, Yu; Qi, Caiyan; Yuan, Mingzhu; He, Yao; Liu, Shishi; Liu, Xiaopei; Wang, Jiaheng; Huang, Lan; Wang, Yan; Baby, Dibin; Wang, David; Zhang, Tao; Qi, Yiping; Zhang, Yong Molecular Plant 2019
8334 10.1016/j.molp.2019.03.016 De Novo Domestication: An Alternative Route Toward New Crops For The Future Fernie, Alisdair R.; Yan, Jianbing Molecular Plant 2019
8335 10.1016/j.molp.2019.08.006 Engineering Broad-Spectrum Bacterial Blight Resistance By Simultaneously Disrupting Variable Tale-Binding Elements Of Multiple Susceptibility Genes In Rice Xu, Zhengyin; Xu, Xiameng; Gong, Qiang; Li, Ziyang; Li, Ying; Wang, Sai; Yang, Yangyang; Ma, Wenxiu; Liu, Longyu; Zhu, Bo; Zou, Lifang; Chen, Gongyou Molecular Plant 2019
8337 10.1016/j.molp.2020.01.010 Base-Editing-Mediated Artificial Evolution Of Osals1 In Planta To Develop Novel Herbicide-Tolerant Rice Germplasms Kuang, Yongjie; Li, Shaofang; Ren, Bin; Yan, Fang, 0000-0002-9471-7867; Spetz, Carl; Li, Xiangju; Zhou, Xueping; Zhou, Huanbin Molecular Plant 2020
8338 10.1016/j.molp.2020.03.010 Plant Prime Editors Enable Precise Gene Editing In Rice Cells Tang, Xu; Sretenovic, Simon; Ren, Qiurong; Jia, Xinyu; Li, Mengke; Fan, Tingting; Yin, Desuo; Xiang, Shuyue; Guo, Yachong; Liu, Li; Zheng, Xuelian; Qi, Yiping; Zhang, Yong, 0000-0003-3704-4835 Molecular Plant 2020
8339 10.1016/j.molp.2020.03.011 Precise Modifications Of Both Exogenous And Endogenous Genes In Rice By Prime Editing Li, Huiyuan; Li, Jingying; Chen, Jilin; Yan, Lei; Xia, Lanqin, 0000-0002-5158-9834 Molecular Plant 2020
8340 10.1016/j.molp.2020.03.012 Versatile Nucleotides Substitution In Plant Using An Improved Prime Editing System Xu, Wen; Zhang, Chengwei; Yang, Yongxing; Zhao, Si; Kang, Guiting; He, Xiaoqing; Song, Jinling; Yang, Jinxiao Molecular Plant 2020
9661 10.1016/j.stem.2019.02.019 Precise Gene Editing Preserves Hematopoietic Stem Cell Function Following Transient P53-Mediated Dna Damage Response Schiroli, Giulia; Conti, Anastasia; Ferrari, Samuele; Della Volpe, Lucrezia; Jacob, Aurelien; Albano, Luisa; Beretta, Stefano; Calabria, Andrea; Vavassori, Valentina; Gasparini, Patrizia; Salataj, Eralda; Ndiaye-Lobry, Delphine; Brombin, Chiara; Chaumeil, Julie; Montini, Eugenio; Merelli, Ivan; Genovese, Pietro; Naldini, Luigi; Di Micco, Raffaella Cell Stem Cell 2019
9664 10.1016/j.stem.2019.04.001 Highly Efficient And Marker-Free Genome Editing Of Human Pluripotent Stem Cells By Crispr-Cas9 Rnp And Aav6 Donor-Mediated Homologous Recombination Martin, Renata M.; Ikeda, Kazuya; Cromer, M. Kyle; Uchida, Nobuko; Nishimura, Toshinobu; Romano, Rosa; Tong, Andrew J.; Lemgart, Viktor T.; Camarena, Joab; Pavel-Dinu, Mara; Sindhu, Camille; Wiebking, Volker; Vaidyanathan, Sriram; Dever, Daniel P.; Bak, Rasmus O.; Laustsen, Anders; Lesch, Benjamin J.; Jakobsen, Martin R.; Sebastiano, Vittorio; Nakauchi, Hiromitsu; Porteus, Matthew H. Cell Stem Cell 2019
10065 10.1016/j.ymthe.2018.10.008 Optimization Of Crispr/Cas9 Delivery To Human Hematopoietic Stem And Progenitor Cells For Therapeutic Genomic Rearrangements Lattanzi, Annalisa; Meneghini, Vasco; Pavani, Giulia; Amor, Fatima; Ramadier, Sophie; Felix, Tristan; Antoniani, Chiara; Masson, Cecile; Alibeu, Olivier; Lee, Ciaran; Porteus, Matthew H.; Bao, Gang; Amendola, Mario; Mavilio, Fulvio; Miccio, Annarita Molecular Therapy 2019
10070 10.1016/j.ymthe.2020.01.005 Treatment Of A Mouse Model Of Als By In Vivo Base Editing Lim, Colin K.W.; Gapinske, Michael; Brooks, Alexandra K.; Woods, Wendy S.; Powell, Jackson E.; Zeballos C., M. Alejandra; Winter, Jackson; Perez-Pinera, Pablo; Gaj, Thomas Molecular Therapy 2020
10156 10.1016/s0140-6736(20)30262-2 Acalabrutinib With Or Without Obinutuzumab Versus Chlorambucil And Obinutuzumab For Treatment-Naive Chronic Lymphocytic Leukaemia (Elevate-Tn): A Randomised, Controlled, Phase 3 Trial Sharman, Jeff P; Egyed, Miklos; Jurczak, Wojciech; Skarbnik, Alan; Pagel, John M; Flinn, Ian W; Kamdar, Manali; Munir, Talha; Walewska, Renata; Corbett, Gillian; Fogliatto, Laura Maria; Herishanu, Yair; Banerji, Versha; Coutre, Steven; Follows, George; Walker, Patricia; Karlsson, Karin; Ghia, Paolo; Janssens, Ann; Cymbalista, Florence; Woyach, Jennifer A; Salles, Gilles; Wierda, William G; Izumi, Raquel; Munugalavadla, Veerendra; Patel, Priti; Wang, Min Hui; Wong, Sofia; Byrd, John C The Lancet 2020
10253 10.1016/s1470-2045(18)30240-7 Quizartinib, An Flt3 Inhibitor, As Monotherapy In Patients With Relapsed Or Refractory Acute Myeloid Leukaemia: An Open-Label, Multicentre, Single-Arm, Phase 2 Trial Cortes, Jorge; Perl, Alexander E; Dohner, Hartmut; Kantarjian, Hagop; Martinelli, Giovanni; Kovacsovics, Tibor; Rousselot, Philippe; Steffen, Bjorn; Dombret, Herve; Estey, Elihu; Strickland, Stephen; Altman, Jessica K; Baldus, Claudia D; Burnett, Alan; Kramer, Alwin; Russell, Nigel; Shah, Neil P; Smith, Catherine C; Wang, Eunice S; Ifrah, Norbert; Gammon, Guy; Trone, Denise; Lazzaretto, Deborah; Levis, Mark The Lancet Oncology 2018
10264 10.1016/s1470-2045(18)30580-1 Measurable Residual Disease-Guided Treatment With Azacitidine To Prevent Haematological Relapse In Patients With Myelodysplastic Syndrome And Acute Myeloid Leukaemia (Relaza2): An Open-Label, Multicentre, Phase 2 Trial Platzbecker, Uwe; Middeke, Jan Moritz; Sockel, Katja; Herbst, Regina; Wolf, Dominik; Baldus, Claudia D; Oelschlagel, Uta; Mutherig, Anke; Fransecky, Lars; Noppeney, Richard; Bug, Gesine; Gotze, Katharina S; Kramer, Alwin; Bochtler, Tilmann; Stelljes, Matthias; Groth, Christoph; Schubert, Antje; Mende, Marika; Stolzel, Friedrich; Borkmann, Christine; Kubasch, Anne Sophie; Von Bonin, Malte; Serve, Hubert; Hanel, Mathias; Duhrsen, Ulrich; Schetelig, Johannes; Rollig, Christoph; Kramer, Michael; Ehninger, Gerhard; Bornhauser, Martin; Thiede, Christian The Lancet Oncology 2018
10273 10.1016/s1470-2045(18)30788-5 Ibrutinib Plus Obinutuzumab Versus Chlorambucil Plus Obinutuzumab In First-Line Treatment Of Chronic Lymphocytic Leukaemia (Illuminate): A Multicentre, Randomised, Open-Label, Phase 3 Trial Moreno, Carol; Greil, Richard; Demirkan, Fatih; Tedeschi, Alessandra; Anz, Bertrand; Larratt, Loree; Simkovic, Martin; Samoilova, Olga; Novak, Jan; Ben-Yehuda, Dina; Strugov, Vladimir; Gill, Devinder; Gribben, John G; Hsu, Emily; Lih, Chih-Jian; Zhou, Cathy; Clow, Fong; James, Danelle F; Styles, Lori; Flinn, Ian W The Lancet Oncology 2019
10286 10.1016/s1470-2045(19)30150-0 Quizartinib Versus Salvage Chemotherapy In Relapsed Or Refractory Flt3-Itd Acute Myeloid Leukaemia (Quantum-R): A Multicentre, Randomised, Controlled, Open-Label, Phase 3 Trial Cortes, Jorge E; Khaled, Samer; Martinelli, Giovanni; Perl, Alexander E; Ganguly, Siddhartha; Russell, Nigel; Kramer, Alwin; Dombret, Herve; Hogge, Donna; Jonas, Brian A; Leung, Anskar Yu-Hung; Mehta, Priyanka; Montesinos, Pau; Radsak, Markus; Sica, Simona; Arunachalam, Meena; Holmes, Melissa; Kobayashi, Ken; Namuyinga, Ruth; Ge, Nanxiang; Yver, Antoine; Zhang, Yufen; Levis, Mark J The Lancet Oncology 2019
10342 10.1016/s1470-2045(20)30441-1 Tazemetostat For Patients With Relapsed Or Refractory Follicular Lymphoma: An Open-Label, Single-Arm, Multicentre, Phase 2 Trial Morschhauser, Franck; Tilly, Herve; Chaidos, Aristeidis; Mckay, Pamela; Phillips, Tycel; Assouline, Sarit; Batlevi, Connie Lee; Campbell, Phillip; Ribrag, Vincent; Damaj, Gandhi Laurent; Dickinson, Michael; Jurczak, Wojciech; Kazmierczak, Maciej; Opat, Stephen; Radford, John; Schmitt, Anna; Yang, Jay; Whalen, Jennifer; Agarwal, Shefali; Adib, Deyaa; Salles, Gilles The Lancet Oncology 2020
10344 10.1016/s1470-2045(20)30443-5 Venetoclax Plus Obinutuzumab Versus Chlorambucil Plus Obinutuzumab For Previously Untreated Chronic Lymphocytic Leukaemia (Cll14): Follow-Up Results From A Multicentre, Open-Label, Randomised, Phase 3 Trial Al-Sawaf, Othman; Zhang, Can; Tandon, Maneesh; Sinha, Arijit; Fink, Anna-Maria; Robrecht, Sandra; Samoylova, Olga; Liberati, Anna M; Pinilla-Ibarz, Javier; Opat, Stephen; Sivcheva, Liliya; Le Du, Katell; Fogliatto, Laura M; Niemann, Carsten U; Weinkove, Robert; Robinson, Sue; Kipps, Thomas J; Tausch, Eugen; Schary, William; Ritgen, Matthias; Wendtner, Clemens-Martin; Kreuzer, Karl-Anton; Eichhorst, Barbara; Stilgenbauer, Stephan; Hallek, Michael; Fischer, Kirsten The Lancet Oncology 2020
10346 10.1016/s1470-2045(20)30455-1 Sorafenib Maintenance In Patients With Flt3-Itd Acute Myeloid Leukaemia Undergoing Allogeneic Haematopoietic Stem-Cell Transplantation: An Open-Label, Multicentre, Randomised Phase 3 Trial Xuan, Li; Wang, Yu; Huang, Fen; Fan, Zhiping; Xu, Yajing; Sun, Jing; Xu, Na; Deng, Lan; Li, Xudong; Liang, Xinquan; Luo, Xiaodan; Shi, Pengcheng; Liu, Hui; Wang, Zhixiang; Jiang, Ling; Yu, Chunzi; Zhou, Xuan; Lin, Ren; Chen, Yan; Tu, Sanfang; Huang, Xiaojun; Liu, Qifa The Lancet Oncology 2020
10516 10.1016/s2352-3026(18)30196-0 Umbralisib In Combination With Ibrutinib In Patients With Relapsed Or Refractory Chronic Lymphocytic Leukaemia Or Mantle Cell Lymphoma: A Multicentre Phase 1<U+2013>1B Study Davids, Matthew S; Kim, Haesook T; Nicotra, Alyssa; Savell, Alexandra; Francoeur, Karen; Hellman, Jeffrey M; Bazemore, Josie; Miskin, Hari P; Sportelli, Peter; Stampleman, Laura; Maegawa, Rodrigo; Rueter, Jens; Boruchov, Adam M; Arnason, Jon E; Jacobson, Caron A; Jacobsen, Eric D; Fisher, David C; Brown, Jennifer R The Lancet Haematology 2019
10517 10.1016/s2352-3026(19)30021-3 Lentiviral Haemopoietic Stem/Progenitor Cell Gene Therapy For Treatment Of Wiskott-Aldrich Syndrome: Interim Results Of A Non-Randomised, Open-Label, Phase 1/2 Clinical Study Ferrua, Francesca; Cicalese, Maria Pia; Galimberti, Stefania; Giannelli, Stefania; Dionisio, Francesca; Barzaghi, Federica; Migliavacca, Maddalena; Bernardo, Maria Ester; Calbi, Valeria; Assanelli, Andrea Angelo; Facchini, Marcella; Fossati, Claudia; Albertazzi, Elena; Scaramuzza, Samantha; Brigida, Immacolata; Scala, Serena; Basso-Ricci, Luca; Pajno, Roberta; Casiraghi, Miriam; Canarutto, Daniele; Salerio, Federica Andrea; Albert, Michael H; Bartoli, Antonella; Wolf, Hermann M; Fiori, Rossana; Silvani, Paolo; Gattillo, Salvatore; Villa, Anna; Biasco, Luca; Dott, Christopher; Culme-Seymour, Emily J; Van Rossem, Koenraad; Atkinson, Gillian; Valsecchi, Maria Grazia; Roncarolo, Maria Grazia; Ciceri, Fabio; Naldini, Luigi; Aiuti, Alessandro The Lancet Haematology 2019
10519 10.1016/s2352-3026(19)30030-4 An Oral Fixed-Dose Combination Of Decitabine And Cedazuridine In Myelodysplastic Syndromes: A Multicentre, Open-Label, Dose-Escalation, Phase 1 Study Savona, Michael R; Odenike, Olatoyosi; Amrein, Philip C; Steensma, David P; Dezern, Amy E; Michaelis, Laura C; Faderl, Stefan; Harb, Wael; Kantarjian, Hagop; Lowder, James; Oganesian, Aram; Azab, Mohammad; Garcia-Manero, Guillermo The Lancet Haematology 2019
10525 10.1016/s2352-3026(20)30210-6 10-Day Decitabine With Venetoclax For Newly Diagnosed Intensive Chemotherapy Ineligible, And Relapsed Or Refractory Acute Myeloid Leukaemia: A Single-Centre, Phase 2 Trial Dinardo, Courtney D; Maiti, Abhishek; Rausch, Caitlin R; Pemmaraju, Naveen; Naqvi, Kiran; Daver, Naval G; Kadia, Tapan M; Borthakur, Gautam; Ohanian, Maro; Alvarado, Yesid; Issa, Ghayas C; Montalban-Bravo, Guillermo; Short, Nicholas J; Yilmaz, Musa; Bose, Prithviraj; Jabbour, Elias J; Takahashi, Koichi; Burger, Jan A; Garcia-Manero, Guillermo; Jain, Nitin; Kornblau, Steven M; Thompson, Philip A; Estrov, Zeev; Masarova, Lucia; Sasaki, Koji; Verstovsek, Srdan; Ferrajoli, Alessandra; Weirda, William G; Wang, Sa A; Konoplev, Sergej; Chen, Zhining; Pierce, Sherry A; Ning, Jing; Qiao, Wei; Ravandi, Farhad; Andreeff, Michael; Welch, John S; Kantarjian, Hagop M; Konopleva, Marina Y The Lancet Haematology 2020
11068 10.1021/acs.jmedchem.9b00687 Guo, Yunhang, 0000-0003-3980-0673; Liu, Ye; Hu, Nan; Yu, Desheng; Zhou, Changyou; Shi, Gongyin; Zhang, Bo; Wei, Min; Liu, Junhua; Luo, Lusong; Tang, Zhiyu; Song, Huipeng; Guo, Yin; Liu, Xuesong; Su, Dan; Zhang, Shuo; Song, Xiaomin; Zhou, Xing; Hong, Yuan; Chen, Shuaishuai; Cheng, Zhenzhen; Young, Steve; Wei, Qiang; Wang, Haisheng; Wang, Qiuwen; Lv, Lei; Wang, Fan; Xu, Haipeng; Sun, Hanzi; Xing, Haimei; Li, Na; Zhang, Wei; Wang, Zhongbo; Liu, Guodong; Sun, Zhijian; Zhou, Dongping; Li, Wei; Liu, Libin; Wang, Lai; Wang, Zhiwei, 0000-0001-8792-9573 Journal Of Medicinal Chemistry 2019
12569 10.1038/nature26155 Evolved Cas9 Variants With Broad Pam Compatibility And High Dna Specificity Hu, Johnny H.; Miller, Shannon M.; Geurts, Maarten H.; Tang, Weixin; Chen, Liwei; Sun, Ning; Zeina, Christina M.; Gao, Xue; Rees, Holly A.; Lin, Zhi; Liu, David R. Nature 2018
12575 10.1038/nbt.4148 Adenine Base Editing In Mouse Embryos And An Adult Mouse Model Of Duchenne Muscular Dystrophy Ryu, Seuk-Min; Koo, Taeyoung; Kim, Kyoungmi; Lim, Kayeong; Baek, Gayoung; Kim, Sang-Tae; Kim, Heon Seok; Kim, Da-Eun; Lee, Hyunji; Chung, Eugene; Kim, Jin-Soo Nature Biotechnology 2018
12576 10.1038/nbt.4172 Improving Cytidine And Adenine Base Editors By Expression Optimization And Ancestral Reconstruction Koblan, Luke W; Doman, Jordan L; Wilson, Christopher, 0000-0002-8012-2440; Levy, Jonathan M, 0000-0002-8061-7953; Tay, Tristan; Newby, Gregory A, 0000-0001-7869-2615; Maianti, Juan Pablo; Raguram, Aditya; Liu, David R Nature Biotechnology 2018
12578 10.1038/nbt.4194 Optimized Base Editors Enable Efficient Editing In Cells, Organoids And Mice Zafra, Maria Paz; Schatoff, Emma M; Katti, Alyna; Foronda, Miguel; Breinig, Marco; Schweitzer, Anabel Y; Simon, Amber; Han, Teng; Goswami, Sukanya; Montgomery, Emma; Thibado, Jordana; Kastenhuber, Edward R; Sanchez-Rivera, Francisco J; Shi, Junwei, 0000-0002-8427-6316; Vakoc, Christopher R; Lowe, Scott W, 0000-0002-5284-9650; Tschaharganeh, Darjus F; Dow, Lukas E Nature Biotechnology 2018
12579 10.1038/nbt.4198 Efficient Base Editing In Methylated Regions With A Human Apobec3A-Cas9 Fusion Wang, Xiao; Li, Jianan; Wang, Ying; Yang, Bei, 0000-0001-5389-3859; Wei, Jia; Wu, Jing; Wang, Ruixuan; Huang, Xingxu; Chen, Jia, 0000-0002-4242-2899; Yang, Li, 0000-0001-8833-7473 Nature Biotechnology 2018
12580 10.1038/nbt.4199 An Apobec3A-Cas9 Base Editor With Minimized Bystander And Off-Target Activities Gehrke, Jason M; Cervantes, Oliver; Clement, M Kendell, 0000-0003-3808-0811; Wu, Yuxuan; Zeng, Jing; Bauer, Daniel E; Pinello, Luca; Joung, J Keith Nature Biotechnology 2018
12588 10.1038/nbt.4261 Efficient C-To-T Base Editing In Plants Using A Fusion Of Ncas9 And Human Apobec3A Zong, Yuan; Song, Qianna; Li, Chao; Jin, Shuai; Zhang, Dingbo; Wang, Yanpeng; Qiu, Jin-Long, 0000-0001-8054-2552; Gao, Caixia, 0000-0003-3169-8248 Nature Biotechnology 2018
12589 10.1038/nbt.4272 De Novo Domestication Of Wild Tomato Using Genome Editing Zsogon, Agustin, 0000-0001-7828-7425; <U+010C>ermak, Toma<U+0161>; Naves, Emmanuel Rezende; Notini, Marcela Morato; Edel, Kai H; Weinl, Stefan; Freschi, Luciano; Voytas, Daniel F; Kudla, Jorg, 0000-0002-8238-767X; Peres, Lazaro Eustaquio Pereira, 0000-0002-8761-5934 Nature Biotechnology 2018
12590 10.1038/nbt.4273 Domestication Of Wild Tomato Is Accelerated By Genome Editing Li, Tingdong; Yang, Xinping; Yu, Yuan; Si, Xiaomin; Zhai, Xiawan; Zhang, Huawei; Dong, Wenxia; Gao, Caixia, 0000-0003-3169-8248; Xu, Cao Nature Biotechnology 2018
12604 10.1038/s41375-018-0312-9 Randomized Comparison Of Low Dose Cytarabine With Or Without Glasdegib In Patients With Newly Diagnosed Acute Myeloid Leukemia Or High-Risk Myelodysplastic Syndrome Leukemia 2018
12605 10.1038/s41375-018-0326-3 Zeijlemaker, Wendelien; Grob, Tim; Meijer, Rosa; Hanekamp, Diana; Kelder, Angele; Carbaat-Ham, Jannemieke C.; Oussoren-Brockhoff, Yvonne J. M.; Snel, Alexander N.; Veldhuizen, Dennis; Scholten, Willemijn J.; Maertens, Johan; Breems, Dimitri A.; Pabst, Thomas; Manz, Markus G., 0000-0002-4676-7931; Van Der Velden, Vincent H. J.; Slomp, Jennichjen; Preijers, Frank; Cloos, Jacqueline; Van De Loosdrecht, Arjan A.; Lowenberg, Bob; Valk, Peter J. M.; Jongen-Lavrencic, Mojca; Ossenkoppele, Gert J.; Schuurhuis, Gerrit J. Leukemia 2018
12606 10.1038/s41375-018-0351-2 Tp53 Mutation Status Divides Myelodysplastic Syndromes With Complex Karyotypes Into Distinct Prognostic Subgroups Haase, Detlef; Stevenson, Kristen E.; Neuberg, Donna, 0000-0003-2566-3145; Maciejewski, Jaroslaw P.; Nazha, Aziz; Sekeres, Mikkael A.; Ebert, Benjamin L.; Garcia-Manero, Guillermo; Haferlach, Claudia; Haferlach, Torsten; Kern, Wolfgang; Ogawa, Seishi; Nagata, Yasunobu; Yoshida, Kenichi; Graubert, Timothy A.; Walter, Matthew J., 0000-0002-7753-1091; List, Alan F.; Komrokji, Rami S.; Padron, Eric; Sallman, David; Papaemmanuil, Elli; Campbell, Peter J.; Savona, Michael R., 0000-0003-3763-5504; Seegmiller, Adam; Ades, Lionel; Fenaux, Pierre; Shih, Lee-Yung, 0000-0003-1866-7922; Bowen, David; Groves, Michael J.; Tauro, Sudhir; Fontenay, Michaela; Kosmider, Olivier; Bar-Natan, Michal; Steensma, David; Stone, Richard; Heuser, Michael; Thol, Felicitas; Cazzola, Mario; Malcovati, Luca; Karsan, Aly; Ganster, Christina; Hellstrom-Lindberg, Eva; Boultwood, Jacqueline; Pellagatti, Andrea, 0000-0002-6122-0221; Santini, Valeria; Quek, Lynn; Vyas, Paresh, 0000-0003-3931-0914; Tuchler, Heinz; Greenberg, Peter L.; Bejar, Rafael, 0000-0002-5603-4598 Leukemia 2019
12607 10.1038/s41375-018-0357-9 Targeting Flt3 Mutations In Aml: Review Of Current Knowledge And Evidence Daver, Naval; Schlenk, Richard F.; Russell, Nigel H.; Levis, Mark J. Leukemia 2019
12610 10.1038/s41375-019-0472-2 Enasidenib, An Inhibitor Of Mutant Idh2 Proteins, Induces Durable Remissions In Older Patients With Newly Diagnosed Acute Myeloid Leukemia Pollyea, Daniel A., 0000-0001-6519-4860; Tallman, Martin S.; De Botton, Stephane; Kantarjian, Hagop M.; Collins, Robert, 0000-0003-0313-2394; Stein, Anthony S.; Frattini, Mark G.; Xu, Qiang; Tosolini, Alessandra; See, Wendy L.; Macbeth, Kyle J.; Agresta, Samuel V.; Attar, Eyal C.; Dinardo, Courtney D., 0000-0001-9003-0390; Stein, Eytan M. Leukemia 2019
12612 10.1038/s41375-019-0602-x Long-Term Efficacy And Safety Of First-Line Ibrutinib Treatment For Patients With Cll/Sll: 5 Years Of Follow-Up From The Phase 3 Resonate-2 Study Burger, Jan A.; Barr, Paul M.; Robak, Tadeusz; Owen, Carolyn; Ghia, Paolo, 0000-0003-3750-7342; Tedeschi, Alessandra; Bairey, Osnat; Hillmen, Peter; Coutre, Steven E.; Devereux, Stephen; Grosicki, Sebastian; Mccarthy, Helen; Simpson, David; Offner, Fritz; Moreno, Carol; Dai, Sandra; Lal, Indu; Dean, James P.; Kipps, Thomas J. Leukemia 2019
12613 10.1038/s41375-019-0612-8 How We Use Venetoclax With Hypomethylating Agents For The Treatment Of Newly Diagnosed Patients With Acute Myeloid Leukemia Jonas, Brian A., 0000-0002-4921-5809; Pollyea, Daniel A., 0000-0001-6519-4860 Leukemia 2019
12616 10.1038/s41375-019-0694-3 Flt3 Inhibitors In Acute Myeloid Leukemia: Ten Frequently Asked Questions Antar, Ahmad I.; Otrock, Zaher K.; Jabbour, Elias; Mohty, Mohamad; Bazarbachi, Ali Leukemia 2020
12708 10.1038/s41421-020-0165-z Efficient Generation Of Mouse Models With The Prime Editing System Liu, Yao; Li, Xiangyang; He, Siting; Huang, Shuhong; Li, Chao; Chen, Yulin; Liu, Zhen; Huang, Xingxu; Wang, Xiaolong Cell Discovery 2020
12784 10.1038/s41467-018-05477-x Directed Evolution Of Crispr-Cas9 To Increase Its Specificity Lee, Jungjoon K., 0000-0002-6798-1363; Jeong, Euihwan; Lee, Joonsun; Jung, Minhee; Shin, Eunji; Kim, Young-Hoon; Lee, Kangin; Jung, Inyoung; Kim, Daesik; Kim, Seokjoong; Kim, Jin-Soo, 0000-0003-4847-1306 Nature Communications 2018
12894 10.1038/s41467-018-07988-z Genome-Wide Profiling Of Adenine Base Editor Specificity By Endov-Seq Liang, Puping, 0000-0003-3593-2599; Xie, Xiaowei; Zhi, Shengyao; Sun, Hongwei; Zhang, Xiya; Chen, Yu; Chen, Yuxi; Xiong, Yuanyan; Ma, Wenbin, 0000-0001-8774-7593; Liu, Dan; Huang, Junjiu; Songyang, Zhou Nature Communications 2019
12897 10.1038/s41467-018-08034-8 Engineering Of High-Precision Base Editors For Site-Specific Single Nucleotide Replacement Tan, Junjie, 0000-0002-9983-1562; Zhang, Fei; Karcher, Daniel; Bock, Ralph, 0000-0001-7502-6940 Nature Communications 2019
12918 10.1038/s41467-018-08263-x Clinical Resistance To Crenolanib In Acute Myeloid Leukemia Due To Diverse Molecular Mechanisms Zhang, Haijiao; Savage, Samantha; Schultz, Anna Reister, 0000-0001-9977-7343; Bottomly, Daniel; White, Libbey, 0000-0003-4409-083X; Segerdell, Erik; Wilmot, Beth, 0000-0003-3579-3592; Mcweeney, Shannon K., 0000-0001-8333-6607; Eide, Christopher A.; Nechiporuk, Tamilla; Carlos, Amy; Henson, Rachel; Lin, Chenwei; Searles, Robert; Ho, Hoang; Lam, Yee Ling; Sweat, Richard; Follit, Courtney; Jain, Vinay; Lind, Evan; Borthakur, Gautam; Garcia-Manero, Guillermo; Ravandi, Farhad; Kantarjian, Hagop M.; Cortes, Jorge; Collins, Robert, 0000-0003-0313-2394; Buelow, Daelynn R.; Baker, Sharyn D.; Druker, Brian J., 0000-0001-8331-8206; Tyner, Jeffrey W. Nature Communications 2019
13022 10.1038/s41467-019-09614-y Gene Correction For Scid-X1 In Long-Term Hematopoietic Stem Cells Pavel-Dinu, Mara; Wiebking, Volker, 0000-0002-9429-5254; Dejene, Beruh T.; Srifa, Waracharee; Mantri, Sruthi; Nicolas, Carmencita E.; Lee, Ciaran, 0000-0002-0789-9149; Bao, Gang; Kildebeck, Eric J.; Punjya, Niraj; Sindhu, Camille; Inlay, Matthew A.; Saxena, Nivedita; Deravin, Suk See; Malech, Harry; Roncarolo, Maria Grazia; Weinberg, Kenneth I.; Porteus, Matthew H., 0000-0002-3850-4648 Nature Communications 2019
13072 10.1038/s41467-019-10363-1 Structures Of Bcl-2 In Complex With Venetoclax Reveal The Molecular Basis Of Resistance Mutations Birkinshaw, Richard W., 0000-0003-1825-0182; Gong, Jia-Nan; Luo, Cindy S.; Lio, Daisy; White, Christine A., 0000-0001-8033-9140; Anderson, Mary Ann; Blombery, Piers; Lessene, Guillaume, 0000-0002-1193-8147; Majewski, Ian J.; Thijssen, Rachel; Roberts, Andrew W., 0000-0002-7341-5720; Huang, David C. S.; Colman, Peter M.; Czabotar, Peter E., 0000-0002-2594-496X Nature Communications 2019
13087 10.1038/s41467-019-10735-7 Crispr-Cas9 Fusion To Dominant-Negative 53Bp1 Enhances Hdr And Inhibits Nhej Specifically At Cas9 Target Sites Jayavaradhan, Rajeswari, 0000-0002-7608-9553; Pillis, Devin M., 0000-0002-4260-8298; Goodman, Michael, 0000-0002-5456-6988; Zhang, Fan; Zhang, Yue; Andreassen, Paul R.; Malik, Punam, 0000-0002-8942-2108 Nature Communications 2019
13192 10.1038/s41467-019-13007-6 Highly Efficient Multiplex Human T Cell Engineering Without Double-Strand Breaks Using Cas9 Base Editors Webber, Beau R., 0000-0002-3950-8747; Lonetree, Cara-Lin; Kluesner, Mitchell G., 0000-0001-5828-9204; Johnson, Matthew J., 0000-0002-1313-1742; Pomeroy, Emily J., 0000-0001-7690-3570; Diers, Miechaleen D.; Lahr, Walker S.; Draper, Garrett M.; Slipek, Nicholas J., 0000-0003-2664-6507; Smeester, Branden A.; Lovendahl, Klaus N., 0000-0002-3871-3570; Mcelroy, Amber N.; Gordon, Wendy R.; Osborn, Mark J.; Moriarity, Branden S. Nature Communications 2019
13459 10.1038/s41551-019-0357-8 Adenine Base Editing In An Adult Mouse Model Of Tyrosinaemia Song, Chun-Qing; Jiang, Tingting; Richter, Michelle; Rhym, Luke H.; Koblan, Luke W.; Zafra, Maria Paz; Schatoff, Emma M.; Doman, Jordan L.; Cao, Yueying; Dow, Lukas E.; Zhu, Lihua Julie, 0000-0001-7416-0590; Anderson, Daniel G; Liu, David R., 0000-0002-9943-7557; Yin, Hao, 0000-0001-9654-5985; Xue, Wen, 0000-0002-9797-8042 Nature Biomedical Engineering 2019
13464 10.1038/s41551-019-0501-5 Cytosine And Adenine Base Editing Of The Brain, Liver, Retina, Heart And Skeletal Muscle Of Mice Via Adeno-Associated Viruses Levy, Jonathan M., 0000-0002-8061-7953; Yeh, Wei-Hsi, 0000-0001-7507-8177; Pendse, Nachiket; Davis, Jessie R.; Hennessey, Erin; Butcher, Rossano; Koblan, Luke W.; Comander, Jason; Liu, Qin; Liu, David R., 0000-0002-9943-7557 Nature Biomedical Engineering 2020
13945 10.1038/s41572-019-0132-x Follicular Lymphoma Carbone, Antonino; Roulland, Sandrine; Gloghini, Annunziata; Younes, Anas; Von Keudell, Gottfried; Lopez-Guillermo, Armando; Fitzgibbon, Jude Nature Reviews Disease Primers 2019
13948 10.1038/s41573-019-0020-9 Gene Therapy Targeting Haematopoietic Stem Cells For Inherited Diseases: Progress And Challenges Cavazzana, Marina, 0000-0002-0264-0891; Bushman, Frederic D.; Miccio, Annarita; Andre-Schmutz, Isabelle; Six, Emmanuelle Nature Reviews Drug Discovery 2019
13962 10.1038/s41576-018-0059-1 Base Editing: Precision Chemistry On The Genome And Transcriptome Of Living Cells Rees, Holly A.; Liu, David R. Nature Reviews Genetics 2018
14066 10.1038/s41586-018-0251-7 Acquired Resistance To Idh Inhibition Through Trans Or Cis Dimer-Interface Mutations Intlekofer, Andrew M.; Shih, Alan H.; Wang, Bo; Nazir, Abbas; Rustenburg, Arien S.; Albanese, Steven K.; Patel, Minal; Famulare, Christopher; Correa, Fabian M.; Takemoto, Naofumi; Durani, Vidushi; Liu, Hui; Taylor, Justin; Farnoud, Noushin; Papaemmanuil, Elli; Cross, Justin R.; Tallman, Martin S.; Arcila, Maria E.; Roshal, Mikhail; Petsko, Gregory A.; Wu, Bin; Choe, Sung; Konteatis, Zenon D.; Biller, Scott A.; Chodera, John D.; Thompson, Craig B.; Levine, Ross L.; Stein, Eytan M. Nature 2018
14196 10.1038/s41586-019-1161-z Transcriptome-Wide Off-Target Rna Editing Induced By Crispr-Guided Dna Base Editors Grunewald, Julian; Zhou, Ronghao; Garcia, Sara P.; Iyer, Sowmya; Lareau, Caleb A.; Aryee, Martin J.; Joung, J. Keith Nature 2019
14218 10.1038/s41586-019-1314-0 Off-Target Rna Mutation Induced By Dna Base Editing And Its Elimination By Mutagenesis Zhou, Changyang; Sun, Yidi; Yan, Rui; Liu, Yajing; Zuo, Erwei; Gu, Chan; Han, Linxiao; Wei, Yu; Hu, Xinde; Zeng, Rong; Li, Yixue; Zhou, Haibo; Guo, Fan; Yang, Hui Nature 2019
14289 10.1038/s41586-019-1711-4 Search-And-Replace Genome Editing Without Double-Strand Breaks Or Donor Dna Anzalone, Andrew V.; Randolph, Peyton B.; Davis, Jessie R.; Sousa, Alexander A.; Koblan, Luke W.; Levy, Jonathan M.; Chen, Peter J.; Wilson, Christopher; Newby, Gregory A.; Raguram, Aditya; Liu, David R. Nature 2019
14490 10.1038/s41587-018-0011-0 Engineered Crispr<U+2013>Cas12A Variants With Increased Activities And Improved Targeting Ranges For Gene, Epigenetic And Base Editing Kleinstiver, Benjamin P., 0000-0002-5469-0655; Sousa, Alexander A.; Walton, Russell T.; Tak, Y. Esther; Hsu, Jonathan Y.; Clement, Kendell; Welch, Moira M.; Horng, Joy E., 0000-0001-7702-7381; Malagon-Lopez, Jose; Scarfo, Irene, 0000-0002-5545-3248; Maus, Marcela V., 0000-0002-7578-0393; Pinello, Luca; Aryee, Martin J., 0000-0002-6848-1344; Joung, J. Keith Nature Biotechnology 2019
14495 10.1038/s41587-019-0050-1 Genome-Wide Target Specificity Of Crispr Rna-Guided Adenine Base Editors Kim, Daesik; Kim, Da-Eun; Lee, Gyeorae; Cho, Sung-Ik; Kim, Jin-Soo, 0000-0003-4847-1306 Nature Biotechnology 2019
14496 10.1038/s41587-019-0065-7 Precise Gene Replacement In Rice By Rna Transcript-Templated Homologous Recombination Li, Shaoya; Li, Jingying; He, Yubing; Xu, Meilian; Zhang, Jiahui; Du, Wenming; Zhao, Yunde, 0000-0002-7224-8449; Xia, Lanqin, 0000-0002-5158-9834 Nature Biotechnology 2019
14504 10.1038/s41587-019-0134-y Circularly Permuted And Pam-Modified Cas9 Variants Broaden The Targeting Scope Of Base Editors Huang, Tony P.; Zhao, Kevin T., 0000-0003-3440-2094; Miller, Shannon M.; Gaudelli, Nicole M.; Oakes, Benjamin L.; Fellmann, Christof, 0000-0002-9545-5723; Savage, David F.; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2019
14507 10.1038/s41587-019-0193-0 Continuous Evolution Of Base Editors With Expanded Target Compatibility And Improved Activity Thuronyi, Benjamin W., 0000-0003-0821-3791; Koblan, Luke W.; Levy, Jonathan M., 0000-0002-8061-7953; Yeh, Wei-Hsi; Zheng, Christine; Newby, Gregory A., 0000-0001-7869-2615; Wilson, Christopher, 0000-0002-8012-2440; Bhaumik, Mantu; Shubina-Oleinik, Olga; Holt, Jeffrey R., 0000-0002-7182-8011; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2019
14513 10.1038/s41587-019-0236-6 Crispr Dna Base Editors With Reduced Rna Off-Target And Self-Editing Activities Grunewald, Julian, 0000-0001-7537-7505; Zhou, Ronghao; Iyer, Sowmya; Lareau, Caleb A., 0000-0003-4179-4807; Garcia, Sara P., 0000-0003-3312-6454; Aryee, Martin J., 0000-0002-6848-1344; Joung, J. Keith, 0000-0001-5630-5645 Nature Biotechnology 2019
14517 10.1038/s41587-019-0267-z Broad-Spectrum Resistance To Bacterial Blight In Rice Using Genome Editing Oliva, Ricardo, 0000-0001-9517-5249; Ji, Chonghui; Atienza-Grande, Genelou; Huguet-Tapia, Jose C.; Perez-Quintero, Alvaro, 0000-0003-3530-8251; Li, Ting, 0000-0001-8273-5593; Eom, Joon-Seob; Li, Chenhao; Nguyen, Hanna, 0000-0002-1654-4921; Liu, Bo; Auguy, Florence; Sciallano, Coline; Luu, Van T.; Dossa, Gerbert S.; Cunnac, Sebastien; Schmidt, Sarah M.; Slamet-Loedin, Inez H.; Vera Cruz, Casiana; Szurek, Boris; Frommer, Wolf B., 0000-0001-6465-0115; White, Frank F., 0000-0002-9905-2454; Yang, Bing, 0000-0002-2293-3384 Nature Biotechnology 2019
14524 10.1038/s41587-019-0337-2 Plant Gene Editing Through De Novo Induction Of Meristems Maher, Michael F., 0000-0003-4134-649X; Nasti, Ryan A.; Vollbrecht, Macy, 0000-0002-5636-1070; Starker, Colby G.; Clark, Matthew D.; Voytas, Daniel F., 0000-0002-4944-1224 Nature Biotechnology 2019
14526 10.1038/s41587-019-0361-2 Rapid Customization Of Solanaceae Fruit Crops For Urban Agriculture Kwon, Choon-Tak, 0000-0002-3589-1662; Heo, Jung; Lemmon, Zachary H.; Capua, Yossi; Hutton, Samuel F.; Van Eck, Joyce; Park, Soon Ju; Lippman, Zachary B., 0000-0001-7668-9025 Nature Biotechnology 2019
14529 10.1038/s41587-019-0393-7 Targeted, Random Mutagenesis Of Plant Genes With Dual Cytosine And Adenine Base Editors Li, Chao; Zhang, Rui; Meng, Xiangbing; Chen, Sha; Zong, Yuan; Lu, Chunju; Qiu, Jin-Long, 0000-0001-8054-2552; Chen, Yu-Hang; Li, Jiayang, 0000-0002-0487-6574; Gao, Caixia, 0000-0003-3169-8248 Nature Biotechnology 2020
14531 10.1038/s41587-020-0412-8 Continuous Evolution Of Spcas9 Variants Compatible With Non-G Pams Miller, Shannon M.; Wang, Tina; Randolph, Peyton B., 0000-0001-6385-364X; Arbab, Mandana; Shen, Max W.; Huang, Tony P.; Matuszek, Zaneta; Newby, Gregory A., 0000-0001-7869-2615; Rees, Holly A.; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2020
14532 10.1038/s41587-020-0414-6 Evaluation And Minimization Of Cas9-Independent Off-Target Dna Editing By Cytosine Base Editors Doman, Jordan L., 0000-0002-9887-0391; Raguram, Aditya; Newby, Gregory A., 0000-0001-7869-2615; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2020
14535 10.1038/s41587-020-0453-z Phage-Assisted Evolution Of An Adenine Base Editor With Improved Cas Domain Compatibility And Activity Richter, Michelle F.; Zhao, Kevin T., 0000-0003-3440-2094; Eton, Elliot, 0000-0002-8980-9310; Lapinaite, Audrone, 0000-0002-9427-9342; Newby, Gregory A., 0000-0001-7869-2615; Thuronyi, Benjamin W.; Wilson, Christopher, 0000-0002-8012-2440; Koblan, Luke W.; Zeng, Jing; Bauer, Daniel E.; Doudna, Jennifer A., 0000-0001-9161-999X; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2020
14536 10.1038/s41587-020-0455-x Prime Genome Editing In Rice And Wheat Lin, Qiupeng; Zong, Yuan; Xue, Chenxiao; Wang, Shengxing; Jin, Shuai; Zhu, Zixu; Wang, Yanpeng; Anzalone, Andrew V.; Raguram, Aditya; Doman, Jordan L., 0000-0002-9887-0391; Liu, David R., 0000-0002-9943-7557; Gao, Caixia, 0000-0003-3169-8248 Nature Biotechnology 2020
14539 10.1038/s41587-020-0491-6 Directed Evolution Of Adenine Base Editors With Increased Activity And Therapeutic Application Gaudelli, Nicole M., 0000-0001-8608-4855; Lam, Dieter K.; Rees, Holly A.; Sola-Esteves, Noris M.; Barrera, Luis A., 0000-0003-0612-6416; Born, David A.; Edwards, Aaron; Gehrke, Jason M.; Lee, Seung-Joo; Liquori, Alexander J.; Murray, Ryan; Packer, Michael S.; Rinaldi, Conrad; Slaymaker, Ian M.; Yen, Jonathan; Young, Lauren E.; Ciaramella, Giuseppe, 0000-0003-3339-7211 Nature Biotechnology 2020
14544 10.1038/s41587-020-0527-y Dual Base Editor Catalyzes Both Cytosine And Adenine Base Conversions In Human Cells Zhang, Xiaohui; Zhu, Biyun; Chen, Liang; Xie, Ling; Yu, Weishi; Wang, Ying; Li, Linxi; Yin, Shuming; Yang, Lei; Hu, Handan; Han, Honghui; Li, Yongmei; Wang, Liren; Chen, Geng; Ma, Xueyun; Geng, Hongquan; Huang, Wanfeng; Pang, Xiufeng; Yang, Zuozhen; Wu, Yuxuan; Siwko, Stefan; Kurita, Ryo; Nakamura, Yukio; Yang, Li, 0000-0001-8833-7473; Liu, Mingyao; Li, Dali, 0000-0002-0046-8493 Nature Biotechnology 2020
14545 10.1038/s41587-020-0535-y A Dual-Deaminase Crispr Base Editor Enables Concurrent Adenine And Cytosine Editing Grunewald, Julian, 0000-0001-7537-7505; Zhou, Ronghao, 0000-0002-3917-0694; Lareau, Caleb A., 0000-0003-4179-4807; Garcia, Sara P., 0000-0003-3312-6454; Iyer, Sowmya; Miller, Bret R., 0000-0002-9872-4642; Langner, Lukas M., 0000-0003-4658-9829; Hsu, Jonathan Y.; Aryee, Martin J., 0000-0002-6848-1344; Joung, J. Keith, 0000-0001-5630-5645 Nature Biotechnology 2020
14547 10.1038/s41587-020-0561-9 Genome Editing With Crispr<U+2013>Cas Nucleases, Base Editors, Transposases And Prime Editors Anzalone, Andrew V.; Koblan, Luke W.; Liu, David R., 0000-0002-9943-7557 Nature Biotechnology 2020
14549 10.1038/s41587-020-0592-2 Glycosylase Base Editors Enable C-To-A And C-To-G Base Changes Zhao, Dongdong, 0000-0001-9691-1308; Li, Ju, 0000-0003-0037-4144; Li, Siwei, 0000-0001-6057-2957; Xin, Xiuqing; Hu, Muzi; Price, Marcus A.; Rosser, Susan J.; Bi, Changhao, 0000-0002-1940-8511; Zhang, Xueli, 0000-0002-8660-4037 Nature Biotechnology 2020
14552 10.1038/s41587-020-0609-x Crispr C-To-G Base Editors For Inducing Targeted Dna Transversions In Human Cells Kurt, Ibrahim C., 0000-0003-3927-0991; Zhou, Ronghao, 0000-0002-3917-0694; Iyer, Sowmya; Garcia, Sara P., 0000-0003-3312-6454; Miller, Bret R., 0000-0002-9872-4642; Langner, Lukas M., 0000-0003-4658-9829; Grunewald, Julian, 0000-0001-7537-7505; Joung, J. Keith, 0000-0001-5630-5645 Nature Biotechnology 2020
14553 10.1038/s41587-020-0677-y Predicting The Efficiency Of Prime Editing Guide Rnas In Human Cells Kim, Hui Kwon, 0000-0003-0694-9244; Yu, Goosang, 0000-0002-3650-1822; Park, Jinman; Min, Seonwoo; Lee, Sungtae; Yoon, Sungroh, 0000-0002-2367-197X; Kim, Hyongbum Henry, 0000-0002-4693-738X Nature Biotechnology 2020
14652 10.1038/s41591-018-0137-0 A High-Fidelity Cas9 Mutant Delivered As A Ribonucleoprotein Complex Enables Efficient Gene Editing In Human Hematopoietic Stem And Progenitor Cells Vakulskas, Christopher A., 0000-0001-8510-4332; Dever, Daniel P.; Rettig, Garrett R., 0000-0003-4634-5787; Turk, Rolf, 0000-0003-1283-9594; Jacobi, Ashley M., 0000-0002-9364-6518; Collingwood, Michael A., 0000-0002-8849-4038; Bode, Nicole M., 0000-0001-7209-303X; Mcneill, Matthew S.; Yan, Shuqi; Camarena, Joab; Lee, Ciaran M., 0000-0002-0789-9149; Park, So Hyun; Wiebking, Volker, 0000-0002-9429-5254; Bak, Rasmus O., 0000-0002-7383-0297; Gomez-Ospina, Natalia, 0000-0002-6740-1154; Pavel-Dinu, Mara; Sun, Wenchao, 0000-0003-4306-2896; Bao, Gang; Porteus, Matthew H.; Behlke, Mark A., 0000-0002-4218-857X Nature Medicine 2018
14655 10.1038/s41591-018-0184-6 In Utero Crispr-Mediated Therapeutic Editing Of Metabolic Genes Rossidis, Avery C.; Stratigis, John D.; Chadwick, Alexandra C.; Hartman, Heather A., 0000-0002-0164-4575; Ahn, Nicholas J.; Li, Haiying; Singh, Kshitiz; Coons, Barbara E.; Li, Li; Lv, Wenjian; Zoltick, Philip W.; Alapati, Deepthi; Zacharias, William; Jain, Rajan; Morrisey, Edward E.; Musunuru, Kiran; Peranteau, William H. Nature Medicine 2018
14660 10.1038/s41591-018-0209-1 Treatment Of A Metabolic Liver Disease By In Vivo Genome Base Editing In Adult Mice Villiger, Lukas; Grisch-Chan, Hiu Man; Lindsay, Helen; Ringnalda, Femke; Pogliano, Chiara B.; Allegri, Gabriella; Fingerhut, Ralph; Haberle, Johannes; Matos, Joao; Robinson, Mark D., 0000-0002-3048-5518; Thony, Beat; Schwank, Gerald, 0000-0003-0767-2953 Nature Medicine 2018
14662 10.1038/s41591-018-0233-1 Venetoclax With Azacitidine Disrupts Energy Metabolism And Targets Leukemia Stem Cells In Patients With Acute Myeloid Leukemia Nature Medicine 2018
14665 10.1038/s41591-018-0243-z Dynamic Molecular Monitoring Reveals That Swi<U+2013>Snf Mutations Mediate Resistance To Ibrutinib Plus Venetoclax In Mantle Cell Lymphoma Agarwal, Rishu, 0000-0002-6713-0403; Chan, Yih-Chih, 0000-0003-2177-5406; Tam, Constantine S.; Hunter, Tane; Vassiliadis, Dane; Teh, Charis E.; Thijssen, Rachel; Yeh, Paul; Wong, Stephen Q.; Ftouni, Sarah; Lam, Enid Y. N.; Anderson, Mary Ann; Pott, Christiane; Gilan, Omer; Bell, Charles C.; Knezevic, Kathy; Blombery, Piers; Rayeroux, Kathleen; Zordan, Adrian; Li, Jason; Huang, David C. S.; Wall, Meaghan, 0000-0001-9711-0705; Seymour, John F.; Gray, Daniel H. D., 0000-0002-8457-8242; Roberts, Andrew W., 0000-0002-7341-5720; Dawson, Mark A., 0000-0002-5464-5029; Dawson, Sarah-Jane, 0000-0002-8276-0374 Nature Medicine 2018
14669 10.1038/s41591-018-0301-6 Intrabone Hematopoietic Stem Cell Gene Therapy For Adult And Pediatric Patients Affected By Transfusion-Dependent Ss-Thalassemia Nature Medicine 2019
14678 10.1038/s41591-019-0401-y Highly Efficient Therapeutic Gene Editing Of Human Hematopoietic Stem Cells Wu, Yuxuan; Zeng, Jing; Roscoe, Benjamin P.; Liu, Pengpeng; Yao, Qiuming; Lazzarotto, Cicera R.; Clement, Kendell; Cole, Mitchel A.; Luk, Kevin; Baricordi, Cristina; Shen, Anne H.; Ren, Chunyan; Esrick, Erica B.; Manis, John P.; Dorfman, David M.; Williams, David A.; Biffi, Alessandra; Brugnara, Carlo, 0000-0001-8192-8713; Biasco, Luca; Brendel, Christian; Pinello, Luca; Tsai, Shengdar Q.; Wolfe, Scot A.; Bauer, Daniel E., 0000-0001-5076-7945 Nature Medicine 2019
14708 10.1038/s41591-019-0735-5 Lentiviral Gene Therapy For X-Linked Chronic Granulomatous Disease Kohn, Donald B., 0000-0003-1840-6087; Booth, Claire; Kang, Elizabeth M.; Pai, Sung-Yun; Shaw, Kit L.; Santilli, Giorgia; Armant, Myriam; Buckland, Karen F., 0000-0001-6989-2228; Choi, Uimook; De Ravin, Suk See; Dorsey, Morna J.; Kuo, Caroline Y.; Leon-Rico, Diego; Rivat, Christine; Izotova, Natalia; Gilmour, Kimberly; Snell, Katie; Dip, Jinhua Xu-Bayford; Darwish, Jinan; Morris, Emma C., 0000-0003-4834-1130; Terrazas, Dayna; Wang, Leo D.; Bauser, Christopher A., 0000-0003-0466-4894; Paprotka, Tobias; Kuhns, Douglas B.; Gregg, John; Raymond, Hayley E.; Everett, John K.; Honnet, Geraldine; Biasco, Luca; Newburger, Peter E.; Bushman, Frederic D., 0000-0003-4740-4056; Grez, Manuel; Gaspar, H. Bobby; Williams, David A.; Malech, Harry L.; Galy, Anne; Thrasher, Adrian J., 0000-0002-6097-6115 Nature Medicine 2020
14718 10.1038/s41591-020-0790-y Therapeutic Base Editing Of Human Hematopoietic Stem Cells Zeng, Jing; Wu, Yuxuan; Ren, Chunyan, 0000-0002-3913-2479; Bonanno, Jasmine; Shen, Anne H.; Shea, Devlin; Gehrke, Jason M.; Clement, Kendell, 0000-0003-3808-0811; Luk, Kevin; Yao, Qiuming; Kim, Rachel; Wolfe, Scot A., 0000-0002-7042-201X; Manis, John P.; Pinello, Luca; Joung, J. Keith; Bauer, Daniel E., 0000-0001-5076-7945 Nature Medicine 2020
14741 10.1038/s41591-020-1008-z Implications Of Tp53 Allelic State For Genome Stability, Clinical Presentation And Outcomes In Myelodysplastic Syndromes Bernard, Elsa, 0000-0002-2057-7187; Nannya, Yasuhito; Hasserjian, Robert P.; Devlin, Sean M.; Tuechler, Heinz, 0000-0002-1568-3436; Medina-Martinez, Juan S.; Yoshizato, Tetsuichi, 0000-0003-4283-2983; Shiozawa, Yusuke; Saiki, Ryunosuke; Malcovati, Luca; Levine, Max F., 0000-0001-5156-9086; Arango, Juan E.; Zhou, Yangyu; Sole, Francesc; Cargo, Catherine A.; Haase, Detlef; Creignou, Maria; Germing, Ulrich; Zhang, Yanming; Gundem, Gunes; Sarian, Araxe; Van De Loosdrecht, Arjan A.; Jadersten, Martin; Tobiasson, Magnus; Kosmider, Olivier; Follo, Matilde Y., 0000-0001-6126-0859; Thol, Felicitas; Pinheiro, Ronald F.; Santini, Valeria; Kotsianidis, Ioannis; Boultwood, Jacqueline, 0000-0002-4330-2928; Santos, Fabio P. S.; Schanz, Julie; Kasahara, Senji; Ishikawa, Takayuki; Tsurumi, Hisashi; Takaori-Kondo, Akifumi, 0000-0001-7678-4284; Kiguchi, Toru; Polprasert, Chantana; Bennett, John M.; Klimek, Virginia M.; Savona, Michael R., 0000-0003-3763-5504; Belickova, Monika, 0000-0002-9158-881X; Ganster, Christina, 0000-0002-7566-5985; Palomo, Laura; Sanz, Guillermo, 0000-0002-2767-8191; Ades, Lionel; Della Porta, Matteo Giovanni; Elias, Harold K.; Smith, Alexandra G.; Werner, Yesenia; Patel, Minal; Viale, Agnes; Vanness, Katelynd; Neuberg, Donna S., 0000-0003-2566-3145; Stevenson, Kristen E.; Menghrajani, Kamal; Bolton, Kelly L.; Fenaux, Pierre; Pellagatti, Andrea; Platzbecker, Uwe; Heuser, Michael, 0000-0001-5318-9044; Valent, Peter; Chiba, Shigeru; Miyazaki, Yasushi; Finelli, Carlo; Voso, Maria Teresa, 0000-0002-6164-4761; Shih, Lee-Yung; Fontenay, Michaela, 0000-0002-5492-6349; Jansen, Joop H.; Cervera, Jose; Atsuta, Yoshiko; Gattermann, Norbert; Ebert, Benjamin L., 0000-0003-0197-5451; Bejar, Rafael, 0000-0002-5603-4598; Greenberg, Peter L.; Cazzola, Mario, 0000-0001-6984-8817; Hellstrom-Lindberg, Eva; Ogawa, Seishi, 0000-0002-7778-5374; Papaemmanuil, Elli, 0000-0003-1709-8983 Nature Medicine 2020
15022 10.1038/s42003-019-0288-7 Crispr/Cas9 Editing Of Endogenous Banana Streak Virus In The B Genome Of Musa Spp. Overcomes A Major Challenge In Banana Breeding Tripathi, Jaindra N.; Ntui, Valentine O.; Ron, Mily; Muiruri, Samwel K.; Britt, Anne; Tripathi, Leena, 0000-0001-5723-4981 Communications Biology 2019
16029 10.1056/nejmoa1705342 Thompson, Alexis A.; Walters, Mark C.; Kwiatkowski, Janet; Rasko, John E.J.; Ribeil, Jean-Antoine; Hongeng, Suradej; Magrin, Elisa; Schiller, Gary J.; Payen, Emmanuel; Semeraro, Michaela; Moshous, Despina; Lefrere, Francois; Puy, Herve; Bourget, Philippe; Magnani, Alessandra; Caccavelli, Laure; Diana, Jean-Sebastien; Suarez, Felipe; Monpoux, Fabrice; Brousse, Valentine; Poirot, Catherine; Brouzes, Chantal; Meritet, Jean-Francois; Pondarre, Corinne; Beuzard, Yves; Chretien, Stany; Lefebvre, Thibaud; Teachey, David T.; Anurathapan, Usanarat; Ho, P. Joy; Von Kalle, Christof; Kletzel, Morris; Vichinsky, Elliott; Soni, Sandeep; Veres, Gabor; Negre, Olivier; Ross, Robert W.; Davidson, David; Petrusich, Alexandria; Sandler, Laura; Asmal, Mohammed; Hermine, Olivier; De Montalembert, Mariane; Hacein-Bey-Abina, Salima; Blanche, Stephane; Leboulch, Philippe; Cavazzana, Marina New England Journal Of Medicine 2018
16032 10.1056/nejmoa1713976 Venetoclax<U+2013>Rituximab In Relapsed Or Refractory Chronic Lymphocytic Leukemia New England Journal Of Medicine 2018
16044 10.1056/nejmoa1716863 Molecular Minimal Residual Disease In Acute Myeloid Leukemia Jongen-Lavrencic, Mojca; Grob, Tim; Hanekamp, Diana; Kavelaars, Francois G.; Al Hinai, Adil; Zeilemaker, Annelieke; Erpelinck-Verschueren, Claudia A.J.; Gradowska, Patrycja L.; Meijer, Rosa; Cloos, Jacqueline; Biemond, Bart J.; Graux, Carlos; Van Marwijk Kooy, Marinus; Manz, Markus G.; Pabst, Thomas; Passweg, Jakob R.; Havelange, Violaine; Ossenkoppele, Gert J.; Sanders, Mathijs A.; Schuurhuis, Gerrit J.; Lowenberg, Bob; Valk, Peter J.M. New England Journal Of Medicine 2018
16046 10.1056/nejmoa1716984 Durable Remissions With Ivosidenib Inidh1-Mutated Relapsed Or Refractory Aml Dinardo, Courtney D.; Stein, Eytan M.; De Botton, Stephane; Roboz, Gail J.; Altman, Jessica K.; Mims, Alice S.; Swords, Ronan; Collins, Robert H.; Mannis, Gabriel N.; Pollyea, Daniel A.; Donnellan, Will; Fathi, Amir T.; Pigneux, Arnaud; Erba, Harry P.; Prince, Gabrielle T.; Stein, Anthony S.; Uy, Geoffrey L.; Foran, James M.; Traer, Elie; Stuart, Robert K.; Arellano, Martha L.; Slack, James L.; Sekeres, Mikkael A.; Willekens, Christophe; Choe, Sung; Wang, Hongfang; Zhang, Vickie; Yen, Katharine E.; Kapsalis, Stephanie M.; Yang, Hua; Dai, David; Fan, Bin; Goldwasser, Meredith; Liu, Hua; Agresta, Sam; Wu, Bin; Attar, Eyal C.; Tallman, Martin S.; Stone, Richard M.; Kantarjian, Hagop M. New England Journal Of Medicine 2018
16061 10.1056/nejmoa1805104 Rituximab Plus Lenalidomide In Advanced Untreated Follicular Lymphoma Morschhauser, Franck; Fowler, Nathan H.; Feugier, Pierre; Bouabdallah, Reda; Tilly, Herve; Palomba, M. Lia; Fruchart, Christophe; Libby, Edward N.; Casasnovas, Rene-Olivier; Flinn, Ian W.; Haioun, Corinne; Maisonneuve, Herve; Ysebaert, Loic; Bartlett, Nancy L.; Bouabdallah, Kamal; Brice, Pauline; Ribrag, Vincent; Daguindau, Nicolas; Le Gouill, Steven; Pica, Gian M.; Martin Garcia-Sancho, Alejandro; Lopez-Guillermo, Armando; Larouche, Jean-Francois; Ando, Kiyoshi; Gomes Da Silva, Maria; Andre, Marc; Zachee, Pierre; Sehn, Laurie H.; Tobinai, Kensei; Cartron, Guillaume; Liu, David; Wang, Jianming; Xerri, Luc; Salles, Gilles A. New England Journal Of Medicine 2018
16083 10.1056/nejmoa1812836 Ibrutinib Regimens Versus Chemoimmunotherapy In Older Patients With Untreated Cll Woyach, Jennifer A.; Ruppert, Amy S.; Heerema, Nyla A.; Zhao, Weiqiang; Booth, Allison M.; Ding, Wei, 0000-0001-9811-4601; Bartlett, Nancy L.; Brander, Danielle M.; Barr, Paul M.; Rogers, Kerry A.; Parikh, Sameer A.; Coutre, Steven; Hurria, Arti; Brown, Jennifer R.; Lozanski, Gerard; Blachly, James S.; Ozer, Hatice G.; Major-Elechi, Brittny; Fruth, Briant; Nattam, Sreenivasa; Larson, Richard A.; Erba, Harry; Litzow, Mark; Owen, Carolyn; Kuzma, Charles; Abramson, Jeremy S.; Little, Richard F.; Smith, Scott E.; Stone, Richard M.; Mandrekar, Sumithra J.; Byrd, John C. New England Journal Of Medicine 2018
16093 10.1056/nejmoa1815281 Venetoclax And Obinutuzumab In Patients With Cll And Coexisting Conditions Fischer, Kirsten; Al-Sawaf, Othman; Bahlo, Jasmin; Fink, Anna-Maria; Tandon, Maneesh; Dixon, Mark; Robrecht, Sandra; Warburton, Simon; Humphrey, Kathryn; Samoylova, Olga; Liberati, Anna M.; Pinilla-Ibarz, Javier; Opat, Stephen; Sivcheva, Liliya; Le Du, Katell; Fogliatto, Laura M.; Niemann, Carsten U.; Weinkove, Robert; Robinson, Sue; Kipps, Thomas J.; Boettcher, Sebastian; Tausch, Eugen; Humerickhouse, Rod; Eichhorst, Barbara; Wendtner, Clemens-Martin; Langerak, Anton W.; Kreuzer, Karl-Anton; Ritgen, Matthias; Goede, Valentin; Stilgenbauer, Stephan; Mobasher, Mehrdad; Hallek, Michael New England Journal Of Medicine 2019
16094 10.1056/nejmoa1815408 Lentiviral Gene Therapy Combined With Low-Dose Busulfan In Infants With Scid-X1 Mamcarz, Ewelina; Zhou, Sheng; Lockey, Timothy; Abdelsamed, Hossam; Cross, Shane J.; Kang, Guolian; Ma, Zhijun; Condori, Jose; Dowdy, Jola; Triplett, Brandon; Li, Chen; Maron, Gabriela; Aldave Becerra, Juan C.; Church, Joseph A.; Dokmeci, Elif; Love, James T.; Da Matta Ain, Ana C.; Van Der Watt, Hedi; Tang, Xing; Janssen, William; Ryu, Byoung Y.; De Ravin, Suk See; Weiss, Mitchell J.; Youngblood, Benjamin; Long-Boyle, Janel R.; Gottschalk, Stephen; Meagher, Michael M.; Malech, Harry L.; Puck, Jennifer M.; Cowan, Morton J.; Sorrentino, Brian P. New England Journal Of Medicine 2019
16099 10.1056/nejmoa1817073 Ibrutinib<U+2013>Rituximab Or Chemoimmunotherapy For Chronic Lymphocytic Leukemia New England Journal Of Medicine 2019
16104 10.1056/nejmoa1900574 Ibrutinib And Venetoclax For First-Line Treatment Of Cll Jain, Nitin; Keating, Michael; Thompson, Philip; Ferrajoli, Alessandra; Burger, Jan; Borthakur, Gautam; Takahashi, Koichi; Estrov, Zeev; Fowler, Nathan; Kadia, Tapan; Konopleva, Marina; Alvarado, Yesid; Yilmaz, Musa; Dinardo, Courtney; Bose, Prithviraj; Ohanian, Maro; Pemmaraju, Naveen; Jabbour, Elias; Sasaki, Koji; Kanagal-Shamanna, Rashmi; Patel, Keyur; Jorgensen, Jeffrey; Garg, Naveen; Wang, Xuemei; Sondermann, Katrina; Cruz, Nichole; Wei, Chongjuan; Ayala, Ana; Plunkett, William; Kantarjian, Hagop; Gandhi, Varsha; Wierda, William New England Journal Of Medicine 2019
16109 10.1056/nejmoa1902688 Gilteritinib Or Chemotherapy For Relapsed Or Refractory Flt3-Mutated Aml Perl, Alexander E.; Martinelli, Giovanni; Cortes, Jorge E.; Neubauer, Andreas; Berman, Ellin; Paolini, Stefania; Montesinos, Pau; Baer, Maria R.; Larson, Richard A.; Ustun, Celalettin; Fabbiano, Francesco; Erba, Harry P.; Di Stasi, Antonio; Stuart, Robert; Olin, Rebecca; Kasner, Margaret; Ciceri, Fabio; Chou, Wen-Chien; Podoltsev, Nikolai; Recher, Christian; Yokoyama, Hisayuki; Hosono, Naoko; Yoon, Sung-Soo; Lee, Je-Hwan; Pardee, Timothy; Fathi, Amir T.; Liu, Chaofeng; Hasabou, Nahla; Liu, Xuan; Bahceci, Erkut; Levis, Mark J. New England Journal Of Medicine 2019
16127 10.1056/nejmoa1908892 Luspatercept In Patients With Lower-Risk Myelodysplastic Syndromes Fenaux, Pierre; Platzbecker, Uwe; Mufti, Ghulam J.; Garcia-Manero, Guillermo; Buckstein, Rena; Santini, Valeria; Diez-Campelo, Maria; Finelli, Carlo; Cazzola, Mario, 0000-0001-6984-8817; Ilhan, Osman; Sekeres, Mikkael A.; Falantes, Jose F.; Arrizabalaga, Beatriz; Salvi, Flavia; Giai, Valentina; Vyas, Paresh; Bowen, David; Selleslag, Dominik; Dezern, Amy E.; Jurcic, Joseph G.; Germing, Ulrich; Gotze, Katharina S.; Quesnel, Bruno; Beyne-Rauzy, Odile; Cluzeau, Thomas; Voso, Maria-Teresa; Mazure, Dominiek; Vellenga, Edo; Greenberg, Peter L.; Hellstrom-Lindberg, Eva; Zeidan, Amer M.; Ades, Lionel; Verma, Amit; Savona, Michael R.; Laadem, Abderrahmane; Benzohra, Aziz; Zhang, Jennie; Rampersad, Anita; Dunshee, Diana R., 0000-0001-8930-1587; Linde, Peter G.; Sherman, Matthew L.; Komrokji, Rami S.; List, Alan F. New England Journal Of Medicine 2020
16132 10.1056/nejmoa1910182 Cappellini, M. Domenica; Viprakasit, Vip; Taher, Ali T.; Georgiev, Pencho; Kuo, Kevin H.M.; Coates, Thomas; Voskaridou, Ersi; Liew, Hong-Keng; Pazgal-Kobrowski, Idit; Forni, G.L.; Perrotta, Silverio; Khelif, Abderrahim; Lal, Ashutosh; Kattamis, Antonis; Vlachaki, Efthymia; Origa, Raffaella; Aydinok, Yesim; Bejaoui, Mohamed; Ho, P. Joy; Chew, Lee-Ping; Bee, Ping-Chong; Lim, Soo-Min; Lu, Meng-Yao; Tantiworawit, Adisak; Ganeva, Penka; Gercheva, Liana; Shah, Farrukh; Neufeld, Ellis J.; Thompson, Alexis; Laadem, Abderrahmane; Shetty, Jeevan K.; Zou, Jun; Zhang, Jennie; Miteva, Dimana; Zinger, Tatiana; Linde, Peter G.; Sherman, Matthew L.; Hermine, Olivier; Porter, John; Piga, Antonio New England Journal Of Medicine 2020
16171 10.1056/nejmoa2004444 Oral Azacitidine Maintenance Therapy For Acute Myeloid Leukemia In First Remission Wei, Andrew H.; Dohner, Hartmut; Pocock, Christopher; Montesinos, Pau; Afanasyev, Boris; Dombret, Herve; Ravandi, Farhad; Sayar, Hamid; Jang, Jun-Ho; Porkka, Kimmo; Selleslag, Dominik; Sandhu, Irwindeep; Turgut, Mehmet; Giai, Valentina; Ofran, Yishai; Kizil Cakar, Merih; Botelho De Sousa, Aida; Rybka, Justyna; Frairia, Chiara; Borin, Lorenza; Beltrami, Germana; <U+010C>ermak, Jaroslav; Ossenkoppele, Gert J.; La Torre, Ignazia; Skikne, Barry; Kumar, Keshava; Dong, Qian; Beach, C.L.; Roboz, Gail J. New England Journal Of Medicine 2020
16184 10.1056/nejmoa2012971 Azacitidine And Venetoclax In Previously Untreated Acute Myeloid Leukemia Dinardo, Courtney D.; Jonas, Brian A.; Pullarkat, Vinod; Thirman, Michael J.; Garcia, Jacqueline S.; Wei, Andrew H.; Konopleva, Marina; Dohner, Hartmut; Letai, Anthony; Fenaux, Pierre; Koller, Elizabeth; Havelange, Violaine; Leber, Brian; Esteve, Jordi; Wang, Jianxiang; Pejsa, Vlatko; Hajek, Roman; Porkka, Kimmo; Illes, Arpad; Lavie, David; Lemoli, Roberto M.; Yamamoto, Kazuhito; Yoon, Sung-Soo; Jang, Jun-Ho; Yeh, Su-Peng; Turgut, Mehmet; Hong, Wan-Jen; Zhou, Ying; Potluri, Jalaja; Pratz, Keith W. New England Journal Of Medicine 2020
16212 10.1056/nejmoa2029392 Post-Transcriptional Genetic Silencing Ofbcl11Ato Treat Sickle Cell Disease Esrick, Erica B.; Lehmann, Leslie E.; Biffi, Alessandra; Achebe, Maureen; Brendel, Christian; Ciuculescu, Marioara F.; Daley, Heather; Mackinnon, Brenda; Morris, Emily; Federico, Amy; Abriss, Daniela; Boardman, Kari; Khelladi, Radia; Shaw, Kit; Negre, Helene; Negre, Olivier; Nikiforow, Sarah; Ritz, Jerome; Pai, Sung-Yun; London, Wendy B.; Dansereau, Colleen; Heeney, Matthew M.; Armant, Myriam; Manis, John P; Williams, David A., 0000-0001-7057-6863 New England Journal Of Medicine 2021
16217 10.1056/nejmoa2031054 Frangoul, Haydar; Altshuler, David; Cappellini, M. Domenica; Chen, Yi-Shan; Domm, Jennifer; Eustace, Brenda K.; Foell, Juergen; De La Fuente, Josu; Grupp, Stephan; Handgretinger, Rupert; Ho, Tony W.; Kattamis, Antonis; Kernytsky, Andrew; Lekstrom-Himes, Julie; Li, Amanda M.; Locatelli, Franco; Mapara, Markus Y.; De Montalembert, Mariane; Rondelli, Damiano; Sharma, Akshay; Sheth, Sujit; Soni, Sandeep; Steinberg, Martin H.; Wall, Donna; Yen, Angela; Corbacioglu, Selim New England Journal Of Medicine 2021
16262 10.1056/nejmra1908213 Treatment Of Chronic Lymphocytic Leukemia Burger, Jan A. New England Journal Of Medicine 2020
17342 10.1093/nar/gkz475 Park, So Hyun; Lee, Ciaran M; Dever, Daniel P; Davis, Timothy H; Camarena, Joab; Srifa, Waracharee; Zhang, Yankai; Paikari, Alireza; Chang, Alicia K; Porteus, Matthew H; Sheehan, Vivien A; Bao, Gang Nucleic Acids Research 2019
18584 10.1111/pbi.12982 Activities And Specificities Of Crispr /Cas9 And Cas12A Nucleases For Targeted Mutagenesis In Maize Plant Biotechnology Journal 2018
18585 10.1111/pbi.12987 Simultaneous Crispr/Cas9-Mediated Editing Of Cassava Eif4E Isoforms Ncbp-1 And Ncbp-2 Reduces Cassava Brown Streak Disease Symptom Severity And Incidence Gomez, Michael A.; Lin, Z. Daniel; Moll, Theodore; Chauhan, Raj Deepika; Hayden, Luke; Renninger, Kelley; Beyene, Getu; Taylor, Nigel J., 0000-0002-5426-2247; Carrington, James C.; Staskawicz, Brian J.; Bart, Rebecca S., 0000-0003-1378-3481 Plant Biotechnology Journal 2018
18586 10.1111/pbi.12993 Expanding The Base Editing Scope In Rice By Using Cas9 Variants Hua, Kai; Tao, Xiaoping; Zhu, Jian-Kang, 0000-0001-5134-731X Plant Biotechnology Journal 2018
18587 10.1111/pbi.13006 Design Of A Bacterial Speck Resistant Tomato By Crispr/Cas9-Mediated Editing Of Sljaz2 Ortigosa, Andres; Gimenez-Ibanez, Selena; Leonhardt, Nathalie; Solano, Roberto, 0000-0001-5459-2417 Plant Biotechnology Journal 2018
18588 10.1111/pbi.13053 Xc As9 Expands The Scope Of Genome Editing With Reduced Efficiency In Rice Wang, Junjie; Meng, Xiangbing; Hu, Xixun; Sun, Tingting; Li, Jiayang; Wang, Kejian, 0000-0002-8385-6714; Yu, Hong, 0000-0002-1748-8693 Plant Biotechnology Journal 2019
18589 10.1111/pbi.13068 Single Transcript Unit Crispr 2.0 Systems For Robust Cas9 And Cas12A Mediated Plant Genome Editing Tang, Xu; Ren, Qiurong; Yang, Lijia; Bao, Yu; Zhong, Zhaohui; He, Yao; Liu, Shishi; Qi, Caiyan; Liu, Binglin; Wang, Yan; Sretenovic, Simon; Zhang, Yingxiao; Zheng, Xuelian; Zhang, Tao; Qi, Yiping; Zhang, Yong, 0000-0003-3704-4835 Plant Biotechnology Journal 2019
18590 10.1111/pbi.13077 Creating Highly Efficient Resistance Against Wheat Dwarf Virus In Barley By Employing Crispr /Cas9 System Kis, Andras; Hamar, Eva; Tholt, Gergely; Ban, Rita; Havelda, Zoltan, 0000-0002-6349-7646 Plant Biotechnology Journal 2019
18591 10.1111/pbi.13095 Establishing Crispr /Cas13A Immune System Conferring Rna Virus Resistance In Both Dicot And Monocot Plants Zhang, Tong, 0000-0002-5725-9510; Zhao, Yaling; Ye, Jiajie; Cao, Xue; Xu, Chenhui; Chen, Biao; An, Hong; Jiao, Yuting; Zhang, Fushun; Yang, Xin; Zhou, Guohui Plant Biotechnology Journal 2019
18592 10.1111/pbi.13096 Mimicking Natural Polymorphism In Eif4E By Crispr-Cas9 Base Editing Is Associated With Resistance To Potyviruses Bastet, Anna; Zafirov, Delyan; Giovinazzo, Nathalie; Guyon-Debast, Anouchka; Nogue, Fabien; Robaglia, Christophe; Gallois, Jean-Luc, 0000-0003-0451-1740 Plant Biotechnology Journal 2019
18593 10.1111/pbi.13102 Zhan, Xiaohui; Zhang, Fengjuan; Zhong, Ziyang; Chen, Ruhao; Wang, Yong; Chang, Ling; Bock, Ralph, 0000-0001-7502-6940; Nie, Bihua; Zhang, Jiang, 0000-0003-3949-3765 Plant Biotechnology Journal 2019
18594 10.1111/pbi.13109 Jia, Hongge; Orbovi<U+0107>, Vladimir; Wang, Nian, 0000-0001-7743-0728 Plant Biotechnology Journal 2019
18595 10.1111/pbi.13113 Plant Biotechnology Journal 2019
18596 10.1111/pbi.13168 Qin, Lei; Li, Jianying; Wang, Qiongqiong; Xu, Zhongping; Sun, Lin; Alariqi, Muna; Manghwar, Hakim; Wang, Guanyin; Li, Bo; Ding, Xiao; Rui, Hangping; Huang, Huimei; Lu, Tianliang; Lindsey, Keith; Daniell, Henry, 0000-0003-4485-1176; Zhang, Xianlong, 0000-0002-7703-524X; Jin, Shuangxia, 0000-0002-1495-9154 Plant Biotechnology Journal 2019
18597 10.1111/pbi.13225 Base Editing In Crops: Current Advances, Limitations And Future Implications Mishra, Rukmini; Joshi, Raj Kumar, 0000-0003-0505-2881; Zhao, Kaijun, 0000-0001-9776-416X Plant Biotechnology Journal 2019
18598 10.1111/pbi.13395 Precision Genome Engineering In Rice Using Prime Editing System Plant Biotechnology Journal 2020
18599 10.1111/pbi.13399 Engineering Herbicide Resistance Via Prime Editing In Rice Butt, Haroon; Rao, Gundra Sivakrishna; Sedeek, Khalid; Aman, Rashid; Kamel, Radwa; Mahfouz, Magdy, 0000-0002-0616-6365 Plant Biotechnology Journal 2020
18646 10.1126/sciadv.aau0766 Minimal Pam Specificity Of A Highly Similar Spcas9 Ortholog Chatterjee, Pranam, 0000-0003-3957-8478; Jakimo, Noah; Jacobson, Joseph M. Science Advances 2018
18701 10.1126/sciadv.aax5717 Analysis And Minimization Of Cellular Rna Editing By Dna Adenine Base Editors Rees, Holly A., 0000-0002-6336-8596; Wilson, Christopher, 0000-0002-8012-2440; Doman, Jordan L.; Liu, David R., 0000-0002-9943-7557 Science Advances 2019
18759 10.1126/science.aas9129 Engineered Crispr-Cas9 Nuclease With Expanded Targeting Space Nishimasu, Hiroshi, 0000-0002-2505-1416; Shi, Xi, 0000-0002-7691-2239; Ishiguro, Soh, 0000-0002-2826-2470; Gao, Linyi; Hirano, Seiichi; Okazaki, Sae; Noda, Taichi, 0000-0003-0260-7861; Abudayyeh, Omar O., 0000-0002-7979-3220; Gootenberg, Jonathan S., 0000-0003-2757-2175; Mori, Hideto, 0000-0003-4849-0056; Oura, Seiya, 0000-0002-7606-732X; Holmes, Benjamin, 0000-0002-1444-445X; Tanaka, Mamoru, 0000-0001-8984-0257; Seki, Motoaki, 0000-0003-4207-1408; Hirano, Hisato; Aburatani, Hiroyuki, 0000-0003-0438-1544; Ishitani, Ryuichiro, 0000-0002-4136-5685; Ikawa, Masahito, 0000-0001-9859-6217; Yachie, Nozomu, 0000-0003-1582-6027; Zhang, Feng, 0000-0003-0178-7995; Nureki, Osamu Science 2018
18875 10.1126/science.aav9973 Cytosine Base Editor Generates Substantial Off-Target Single-Nucleotide Variants In Mouse Embryos Zuo, Erwei, 0000-0002-7094-0933; Sun, Yidi, 0000-0002-4191-2917; Wei, Wu, 0000-0001-5643-8739; Yuan, Tanglong, 0000-0003-4670-2625; Ying, Wenqin, 0000-0001-5711-5923; Sun, Hao; Yuan, Liyun, 0000-0001-9122-6782; Steinmetz, Lars M., 0000-0002-3962-2865; Li, Yixue, 0000-0002-1198-7176; Yang, Hui, 0000-0003-3590-722X Science 2019
18897 10.1126/science.aaw7166 Cytosine, But Not Adenine, Base Editors Induce Genome-Wide Off-Target Mutations In Rice Jin, Shuai, 0000-0003-4314-1834; Zong, Yuan, 0000-0003-0576-6614; Gao, Qiang, 0000-0002-9323-1101; Zhu, Zixu, 0000-0003-4068-0082; Wang, Yanpeng, 0000-0003-1577-6883; Qin, Peng, 0000-0001-9046-5423; Liang, Chengzhi, 0000-0001-8913-3552; Wang, Daowen, 0000-0002-6230-8735; Qiu, Jin-Long; Zhang, Feng, 0000-0002-3539-3655; Gao, Caixia Science 2019
18992 10.1126/science.aba8853 Unconstrained Genome Targeting With Near-Pamless Engineered Crispr-Cas9 Variants Walton, Russell T., 0000-0002-0546-474X; Christie, Kathleen A., 0000-0002-8272-6264; Whittaker, Madelynn N., 0000-0002-3382-1134; Kleinstiver, Benjamin P., 0000-0002-5469-0655 Science 2020
19094 10.1126/scitranslmed.aax2863 Inhibition Of Mitochondrial Translation Overcomes Venetoclax Resistance In Aml Through Activation Of The Integrated Stress Response Sharon, David, 0000-0002-0443-3167; Cathelin, Severine; Mirali, Sara; Di Trani, Justin M., 0000-0003-4764-4009; Yanofsky, David J., 0000-0002-4358-7476; Keon, Kristine A., 0000-0001-8185-3803; Rubinstein, John L., 0000-0003-0566-2209; Schimmer, Aaron D.; Ketela, Troy; Chan, Steven M., 0000-0002-4354-0731 Science Translational Medicine 2019
19350 10.1146/annurev-arplant-050718-100049 Crispr/Cas Genome Editing And Precision Plant Breeding In Agriculture Chen, Kunling; Wang, Yanpeng; Zhang, Rui; Zhang, Huawei; Gao, Caixia Annual Review Of Plant Biology 2019
19518 10.1158/1078-0432.ccr-19-2856 Ibrutinib Treatment For First-Line And Relapsed/Refractory Chronic Lymphocytic Leukemia: Final Analysis Of The Pivotal Phase Ib/Ii Pcyc-1102 Study Byrd, John C.; Furman, Richard R.; Coutre, Steven E.; Flinn, Ian W.; Burger, Jan A.; Blum, Kristie; Sharman, Jeff P.; Wierda, William; Zhao, Weiqiang; Heerema, Nyla A.; Luan, Ying; Liu, Emily A.; Dean, James P.; O’Brien, Susan Clinical Cancer Research 2020
19534 10.1158/2159-8290.cd-18-0877 Isoform Switching As A Mechanism Of Acquired Resistance To Mutant Isocitrate Dehydrogenase Inhibition Harding, James J.; Lowery, Maeve A.; Shih, Alan H.; Schvartzman, Juan M., 0000-0002-8036-1361; Hou, Shengqi; Famulare, Christopher; Patel, Minal; Roshal, Mikhail; Do, Richard K., 0000-0002-6554-0310; Zehir, Ahmet, 0000-0001-5406-4104; You, Daoqi; Selcuklu, S. Duygu; Viale, Agnes; Tallman, Martin S.; Hyman, David M.; Reznik, Ed, 0000-0002-6511-5947; Finley, Lydia W.S., 0000-0003-4023-7574; Papaemmanuil, Elli; Tosolini, Alessandra; Frattini, Mark G.; Macbeth, Kyle J.; Liu, Guowen; Fan, Bin; Choe, Sung; Wu, Bin; Janjigian, Yelena Y.; Mellinghoff, Ingo K.; Diaz, Luis A.; Levine, Ross L.; Abou-Alfa, Ghassan K., 0000-0002-1522-8054; Stein, Eytan M.; Intlekofer, Andrew M. Cancer Discovery 2018
19538 10.1158/2159-8290.cd-18-1119 Acquisition Of The Recurrent Gly101Val Mutation In Bcl2 Confers Resistance To Venetoclax In Patients With Progressive Chronic Lymphocytic Leukemia Blombery, Piers; Anderson, Mary Ann; Gong, Jia-Nan; Thijssen, Rachel; Birkinshaw, Richard W., 0000-0003-1825-0182; Thompson, Ella R.; Teh, Charis E.; Nguyen, Tamia; Xu, Zhen; Flensburg, Christoffer; Lew, Thomas E.; Majewski, Ian J.; Gray, Daniel H.D.; Westerman, David A., 0000-0002-9288-9817; Tam, Constantine S.; Seymour, John F., 0000-0003-2188-6835; Czabotar, Peter E.; Huang, David C.S., 0000-0002-3101-4873; Roberts, Andrew W., 0000-0002-7341-5720 Cancer Discovery 2018
19542 10.1158/2159-8290.cd-18-1453 Clonal Selection With Ras Pathway Activation Mediates Secondary Clinical Resistance To Selective Flt3 Inhibition In Acute Myeloid Leukemia Mcmahon, Christine M.; Ferng, Timothy; Canaani, Jonathan; Wang, Eunice S.; Morrissette, Jennifer J.D., 0000-0001-9460-7177; Eastburn, Dennis J.; Pellegrino, Maurizio, 0000-0002-2838-2157; Durruthy-Durruthy, Robert; Watt, Christopher D.; Asthana, Saurabh; Lasater, Elisabeth A.; Defilippis, Rosaanna; Peretz, Cheryl A.C.; Mcgary, Lisa H.F.; Deihimi, Safoora; Logan, Aaron C.; Luger, Selina M.; Shah, Neil P.; Carroll, Martin; Smith, Catherine C.; Perl, Alexander E., 0000-0002-1463-2231 Cancer Discovery 2019
19545 10.1158/2159-8290.cd-19-0117 Targeting Mitochondrial Structure Sensitizes Acute Myeloid Leukemia To Venetoclax Treatment Chen, Xufeng; Glytsou, Christina, 0000-0002-6260-338X; Zhou, Hua; Narang, Sonali; Reyna, Denis E.; Lopez, Andrea; Sakellaropoulos, Theodore, 0000-0001-9946-9498; Gong, Yixiao; Kloetgen, Andreas; Yap, Yoon Sing; Wang, Eric; Gavathiotis, Evripidis, 0000-0001-6319-8331; Tsirigos, Aristotelis, 0000-0002-7512-8477; Tibes, Raoul; Aifantis, Iannis Cancer Discovery 2019
19546 10.1158/2159-8290.cd-19-0125 The Tp53 Apoptotic Network Is A Primary Mediator Of Resistance To Bcl2 Inhibition In Aml Cells Nechiporuk, Tamilla; Kurtz, Stephen E.; Nikolova, Olga, 0000-0001-8105-2440; Liu, Tingting; Jones, Courtney L.; D’Alessandro, Angelo; Culp-Hill, Rachel; D’Almeida, Amanda; Joshi, Sunil K.; Rosenberg, Mara, 0000-0001-6400-3161; Tognon, Cristina E.; Danilov, Alexey V.; Druker, Brian J., 0000-0001-8331-8206; Chang, Bill H., 0000-0003-3783-1820; Mcweeney, Shannon K; Tyner, Jeffrey W., 0000-0002-2133-0960 Cancer Discovery 2019
19554 10.1158/2159-8290.cd-19-0710 Monocytic Subclones Confer Resistance To Venetoclax-Based Therapy In Patients With Acute Myeloid Leukemia Pei, Shanshan; Pollyea, Daniel A., 0000-0001-6519-4860; Gustafson, Annika, 0000-0002-3796-1222; Stevens, Brett M.; Minhajuddin, Mohammad; Fu, Rui, 0000-0001-8183-4549; Riemondy, Kent A., 0000-0003-0750-1273; Gillen, Austin E.; Sheridan, Ryan M., 0000-0003-4012-3147; Kim, Jihye, 0000-0002-0338-2329; Costello, James C., 0000-0003-3158-9682; Amaya, Maria L.; Inguva, Anagha; Winters, Amanda, 0000-0001-7916-7505; Ye, Haobin; Krug, Anna; Jones, Courtney L.; Adane, Biniam; Khan, Nabilah; Ponder, Jessica; Schowinsky, Jeffrey; Abbott, Diana; Hammes, Andrew; Myers, Jason R., 0000-0002-0341-0860; Ashton, John M.; Nemkov, Travis; D’Alessandro, Angelo, 0000-0002-2258-6490; Gutman, Jonathan A.; Ramsey, Haley E.; Savona, Michael R., 0000-0003-3763-5504; Smith, Clayton A., 0000-0001-6478-4244; Jordan, Craig T., 0000-0003-0869-3465 Cancer Discovery 2020
19893 10.1182/blood-2017-09-806398 Iwcll Guidelines For Diagnosis, Indications For Treatment, Response Assessment, And Supportive Management Of Cll Blood 2018
19894 10.1182/blood-2018-02-829911 Measurable Residual Disease Monitoring By Ngs Before Allogeneic Hematopoietic Cell Transplantation In Aml Thol, Felicitas; Gabdoulline, Razif; Liebich, Alessandro; Klement, Piroska; Schiller, Johannes; Kandziora, Christian; Hambach, Lothar; Stadler, Michael; Koenecke, Christian; Flintrop, Madita; Pankratz, Mira; Wichmann, Martin; Neziri, Blerina; Buttner, Konstantin; Heida, Bennet; Klesse, Sabrina; Chaturvedi, Anuhar; Kloos, Arnold; Gohring, Gudrun; Schlegelberger, Brigitte; Gaidzik, Verena I.; Bullinger, Lars; Fiedler, Walter; Heim, Albert; Hamwi, Iyas; Eder, Matthias; Krauter, Jurgen; Schlenk, Richard F.; Paschka, Peter; Dohner, Konstanze; Dohner, Hartmut; Ganser, Arnold; Heuser, Michael Blood 2018
19896 10.1182/blood-2018-05-850461 The Phase 3 Duo Trial: Duvelisib Vs Ofatumumab In Relapsed And Refractory Cll/Sll Flinn, Ian W.; Hillmen, Peter; Montillo, Marco; Nagy, Zsolt; Illes, Arpad; Etienne, Gabriel; Delgado, Julio; Kuss, Bryone J.; Tam, Constantine S.; Gasztonyi, Zoltan; Offner, Fritz; Lunin, Scott; Bosch, Francesco; Davids, Matthew S.; Lamanna, Nicole; Jaeger, Ulrich; Ghia, Paolo; Cymbalista, Florence; Portell, Craig A.; Skarbnik, Alan P.; Cashen, Amanda F.; Weaver, David T.; Kelly, Virginia M.; Turnbull, Barry; Stilgenbauer, Stephan Blood 2018
19899 10.1182/blood-2018-08-868752 Venetoclax Combined With Decitabine Or Azacitidine In Treatment-Naive, Elderly Patients With Acute Myeloid Leukemia Dinardo, Courtney D.; Pratz, Keith; Pullarkat, Vinod; Jonas, Brian A.; Arellano, Martha; Becker, Pamela S.; Frankfurt, Olga; Konopleva, Marina; Wei, Andrew H.; Kantarjian, Hagop M.; Xu, Tu; Hong, Wan-Jen; Chyla, Brenda; Potluri, Jalaja; Pollyea, Daniel A.; Letai, Anthony Blood 2019
19900 10.1182/blood-2018-08-869008 Molecular Remission And Response Patterns In Patients With Mutant-Idh2 Acute Myeloid Leukemia Treated With Enasidenib Stein, Eytan M.; Dinardo, Courtney D.; Fathi, Amir T.; Pollyea, Daniel A.; Stone, Richard M.; Altman, Jessica K.; Roboz, Gail J.; Patel, Manish R.; Collins, Robert; Flinn, Ian W.; Sekeres, Mikkael A.; Stein, Anthony S.; Kantarjian, Hagop M.; Levine, Ross L.; Vyas, Paresh; Macbeth, Kyle J.; Tosolini, Alessandra; Vanoostendorp, Jason; Xu, Qiang; Gupta, Ira; Lila, Thomas; Risueno, Alberto; Yen, Katharine E.; Wu, Bin; Attar, Eyal C.; Tallman, Martin S.; De Botton, Stephane Blood 2019
19901 10.1182/blood-2018-08-869453 Midostaurin Added To Chemotherapy And Continued Single-Agent Maintenance Therapy In Acute Myeloid Leukemia With Flt3-Itd Schlenk, Richard F., 0000-0003-2215-2059; Weber, Daniela; Fiedler, Walter; Salih, Helmut R.; Wulf, Gerald; Salwender, Hans; Schroeder, Thomas; Kindler, Thomas; Lubbert, Michael; Wolf, Dominik; Westermann, Jorg; Kraemer, Doris; Gotze, Katharina S., 0000-0002-6276-8002; Horst, Heinz-August; Krauter, Jurgen; Girschikofsky, Michael; Ringhoffer, Mark; Sudhoff, Thomas; Held, Gerhard; Derigs, Hans-Gunter; Schroers, Roland; Greil, Richard; Grieshammer, Martin; Lange, Elisabeth; Burchardt, Alexander; Martens, Uwe; Hertenstein, Bernd; Marretta, Lore; Heuser, Michael; Thol, Felicitas; Gaidzik, Verena I.; Herr, Wolfgang; Krzykalla, Julia; Benner, Axel, 0000-0002-7238-6956; Dohner, Konstanze; Ganser, Arnold; Paschka, Peter; Dohner, Hartmut Blood 2019
19902 10.1182/blood-2018-08-870238 Long-Term Follow-Up Of The Resonate Phase 3 Trial Of Ibrutinib Vs Ofatumumab Blood 2019
19904 10.1182/blood-2018-10-844696 Treatment Of Mds Platzbecker, Uwe Blood 2019
19905 10.1182/blood-2018-10-879429 Randomized Trial Of Ibrutinib Vs Ibrutinib Plus Rituximab In Patients With Chronic Lymphocytic Leukemia Blood 2019
19906 10.1182/blood-2018-10-879866 Azacitidine Maintenance After Intensive Chemotherapy Improves Dfs In Older Aml Patients Huls, Gerwin; Chitu, Dana A.; Havelange, Violaine; Jongen-Lavrencic, Mojca; Van De Loosdrecht, Arjan A.; Biemond, Bart J.; Sinnige, Harm; Hodossy, Beata; Graux, Carlos; Kooy, Rien Van Marwijk; De Weerdt, Okke; Breems, Dimitri; Klein, Saskia; Kuball, Jurgen; Deeren, Dries; Terpstra, Wim; Vekemans, Marie-Christiane; Ossenkoppele, Gert J.; Vellenga, Edo; Lowenberg, Bob Blood 2019
19917 10.1182/blood-2019-125579 Apr-246 Combined With Azacitidine (Aza) In Tp53 Mutated Myelodysplastic Syndrome (Mds) And Acute Myeloid Leukemia (Aml). A Phase 2 Study By The Groupe Francophone Des Myelodysplasies (Gfm) Cluzeau, Thomas; Sebert, Marie; Rahme, Ramy; Cuzzubbo, Stefania; Walter-Petrich, Anouk; Lehmann Che, Jacqueline; Peterlin, Pierre; Beve, Blandine; Attalah, Habiba; Chermat, Fatiha; Miekoutima, Elsa; Beyne-Rauzy, Odile; Recher, Christian; Stamatoullas, Aspasia; Willems, Lise; Raffoux, Emmanuel; Berthon, Celine; Quesnel, Bruno; Carpentier, Antoine; Sallman, David A; Chevret, Sylvie; Ades, Lionel; Fenaux, Pierre Blood 2019
19918 10.1182/blood-2019-126271 The First-In-Class Anti-Cd47 Antibody Magrolimab (5F9) In Combination With Azacitidine Is Effective In Mds And Aml Patients: Ongoing Phase 1B Results Sallman, David A; Asch, Adam S.; Al Malki, Monzr M.; Lee, Daniel J.; Donnellan, William B.; Marcucci, Guido; Kambhampati, Suman; Daver, Naval G.; Garcia-Manero, Guillermo; Komrokji, Rami S.; Van Elk, Joanna; Lin, Ming; Volkmer, Jens-Peter; Takimoto, Chris H; Chao, Mark; Vyas, Paresh Blood 2019
19920 10.1182/blood-2019-132405 The Quazar Aml-001 Maintenance Trial: Results Of A Phase Iii International, Randomized, Double-Blind, Placebo-Controlled Study Of Cc-486 (Oral Formulation Of Azacitidine) In Patients With Acute Myeloid Leukemia (Aml) In First Remission Wei, Andrew H.; Dohner, Hartmut; Pocock, Christopher; Montesinos, Pau; Afanasyev, Boris; Dombret, Herve; Ravandi, Farhad; Sayar, Hamid; Jang, Jun Ho; Porkka, Kimmo; Selleslag, Dominik; Sandhu, Irwindeep; Turgut, Mehmet; Giai, Valentina; Ofran, Yishai; Kizil Cakar, Merih; Botelho De Sousa, Aida; Rybka, Justyna; Frairia, Chiara; Borin, Lorenza; Beltrami, Germana; Cermak, Jaroslav; Ossenkoppele, Gert J.; La Torre, Ignazia; Skikne, Barry; Kumar, Keshava; Dong, Qian; Beach, Cl; Roboz, Gail J. Blood 2019
19921 10.1182/blood.2018882555 Efficacy Of Venetoclax In Relapsed Chronic Lymphocytic Leukemia Is Influenced By Disease And Response Variables Roberts, Andrew W., 0000-0002-7341-5720; Ma, Shuo; Kipps, Thomas J.; Coutre, Steven E.; Davids, Matthew S.; Eichhorst, Barbara; Hallek, Michael; Byrd, John C.; Humphrey, Kathryn; Zhou, Lang; Chyla, Brenda; Nielsen, Jacqueline; Potluri, Jalaja; Kim, Su Young; Verdugo, Maria; Stilgenbauer, Stephan; Wierda, William G.; Seymour, John F., 0000-0003-2188-6835 Blood 2019
19922 10.1182/blood.2018884940 Acalabrutinib Monotherapy In Patients With Relapsed/Refractory Chronic Lymphocytic Leukemia: Updated Phase 2 Results Blood 2020
19923 10.1182/blood.2018886960 Gimema Aml1310 Trial Of Risk-Adapted, Mrd-Directed Therapy For Young Adults With Newly Diagnosed Acute Myeloid Leukemia Venditti, Adriano, 0000-0002-0245-0553; Piciocchi, Alfonso, 0000-0001-8648-885X; Candoni, Anna; Melillo, Lorella; Calafiore, Valeria; Cairoli, Roberto; De Fabritiis, Paolo; Storti, Gabriella; Salutari, Prassede; Lanza, Francesco; Martinelli, Giovanni; Luppi, Mario; Mazza, Patrizio; Martelli, Maria Paola; Cuneo, Antonio; Albano, Francesco, 0000-0001-7926-6052; Fabbiano, Francesco; Tafuri, Agostino; Chierichini, Anna; Tieghi, Alessia; Fracchiolla, Nicola Stefano; Capelli, Debora; Foa, Robin; Alati, Caterina; La Sala, Edoardo; Fazi, Paola; Vignetti, Marco, 0000-0003-1278-604X; Maurillo, Luca; Buccisano, Francesco, 0000-0003-4320-9253; Del Principe, Maria Ilaria; Irno-Consalvo, Maria; Ottone, Tiziana, 0000-0003-1936-3592; Lavorgna, Serena; Voso, Maria Teresa, 0000-0002-6164-4761; Lo-Coco, Francesco; Arcese, William; Amadori, Sergio Blood 2019
19929 10.1182/blood.2019000840 Hypertension And Incident Cardiovascular Events Following Ibrutinib Initiation Dickerson, Tyler; Wiczer, Tracy; Waller, Allyson; Philippon, Jennifer; Porter, Kyle; Haddad, Devin, 0000-0003-1884-7720; Guha, Avirup, 0000-0003-0253-1174; Rogers, Kerry A., 0000-0001-5748-7874; Bhat, Seema; Byrd, John C.; Woyach, Jennifer A.; Awan, Farrukh, 0000-0003-1813-9812; Addison, Daniel, 0000-0002-9113-8333 Blood 2019
19931 10.1182/blood.2019001160 Phase 1 Study Of The Selective Btk Inhibitor Zanubrutinib In B-Cell Malignancies And Safety And Efficacy Evaluation In Cll Tam, Constantine S., 0000-0002-9759-5017; Trotman, Judith, 0000-0001-8009-4593; Opat, Stephen; Burger, Jan A., 0000-0002-6177-7572; Cull, Gavin; Gottlieb, David; Harrup, Rosemary; Johnston, Patrick B.; Marlton, Paula; Munoz, Javier; Seymour, John F., 0000-0003-2188-6835; Simpson, David, 0000-0002-9768-7413; Tedeschi, Alessandra; Elstrom, Rebecca; Yu, Yiling; Tang, Zhiyu; Han, Lynn; Huang, Jane; Novotny, William; Wang, Lai; Roberts, Andrew W., 0000-0002-7341-5720 Blood 2019
19932 10.1182/blood.2019001239 How I Treat Acute Myeloid Leukemia In The Era Of New Drugs Dinardo, Courtney D., 0000-0001-9003-0390; Wei, Andrew H., 0000-0002-7514-3298 Blood 2020
19935 10.1182/blood.2019002140 Ivosidenib Induces Deep Durable Remissions In Patients With Newly Diagnosed Idh1-Mutant Acute Myeloid Leukemia Roboz, Gail J., 0000-0002-0384-3658; Dinardo, Courtney D., 0000-0001-9003-0390; Stein, Eytan M.; De Botton, Stephane, 0000-0002-8126-4942; Mims, Alice S.; Prince, Gabrielle T.; Altman, Jessica K.; Arellano, Martha L.; Donnellan, Will; Erba, Harry P., 0000-0003-1093-2189; Mannis, Gabriel N.; Pollyea, Daniel A., 0000-0001-6519-4860; Stein, Anthony S.; Uy, Geoffrey L.; Watts, Justin M.; Fathi, Amir T., 0000-0003-4907-6447; Kantarjian, Hagop M.; Tallman, Martin S.; Choe, Sung; Dai, David; Fan, Bin; Wang, Hongfang; Zhang, Vickie; Yen, Katharine E.; Kapsalis, Stephanie M.; Hickman, Denice; Liu, Hua; Agresta, Samuel V.; Wu, Bin, 0000-0001-9232-4456; Attar, Eyal C.; Stone, Richard M. Blood 2020
19938 10.1182/blood.2019003988 Molecular Patterns Of Response And Treatment Failure After Frontline Venetoclax Combinations In Older Patients With Aml Dinardo, C. D., 0000-0001-9003-0390; Tiong, I. S., 0000-0001-7417-4343; Quaglieri, A., 0000-0002-3660-6990; Macraild, S.; Loghavi, S., 0000-0001-8980-3202; Brown, F. C., 0000-0001-9711-9769; Thijssen, R.; Pomilio, G.; Ivey, A.; Salmon, J. M.; Glytsou, C., 0000-0002-6260-338X; Fleming, S. A.; Zhang, Q.; Ma, H.; Patel, K. P., 0000-0001-5081-2427; Kornblau, S. M.; Xu, Z.; Chua, C. C.; Chen, Xufeng, 0000-0001-8325-971X; Blombery, P.; Flensburg, C.; Cummings, N.; Aifantis, I.; Kantarjian, H., 0000-0002-1908-3307; Huang, D. C. S., 0000-0002-3101-4873; Roberts, A. W.; Majewski, I. J., 0000-0002-6087-635X; Konopleva, M., 0000-0002-9347-2212; Wei, A. H., 0000-0002-7514-3298 Blood 2020
19939 10.1182/blood.2019004143 Oral Cedazuridine/Decitabine For Mds And Cmml: A Phase 2 Pharmacokinetic/Pharmacodynamic Randomized Crossover Study Blood 2020
19940 10.1182/blood.2019898114 Cysteine Depletion Targets Leukemia Stem Cells Through Inhibition Of Electron Transport Complex Ii Blood 2019
19941 10.1182/blood.2020004850 Sf3B1-Mutant Mds As A Distinct Disease Subtype: A Proposal From The International Working Group For The Prognosis Of Mds Malcovati, Luca; Stevenson, Kristen; Papaemmanuil, Elli; Neuberg, Donna; Bejar, Rafael, 0000-0002-5603-4598; Boultwood, Jacqueline, 0000-0002-4330-2928; Bowen, David T.; Campbell, Peter J.; Ebert, Benjamin L.; Fenaux, Pierre; Haferlach, Torsten; Heuser, Michael; Jansen, Joop H.; Komrokji, Rami S.; Maciejewski, Jaroslaw P.; Walter, Matthew J.; Fontenay, Michaela; Garcia-Manero, Guillermo; Graubert, Timothy A.; Karsan, Aly; Meggendorfer, Manja; Pellagatti, Andrea; Sallman, David A.; Savona, Michael R., 0000-0003-3763-5504; Sekeres, Mikkael A.; Steensma, David P., 0000-0001-5130-9284; Tauro, Sudhir, 0000-0002-7236-970X; Thol, Felicitas; Vyas, Paresh, 0000-0003-3931-0914; Van De Loosdrecht, Arjan A.; Haase, Detlef; Tuchler, Heinz; Greenberg, Peter L.; Ogawa, Seishi, 0000-0002-7778-5374; Hellstrom-Lindberg, Eva; Cazzola, Mario Blood 2020
19942 10.1182/blood.2020004856 Venetoclax Plus Ldac For Newly Diagnosed Aml Ineligible For Intensive Chemotherapy: A Phase 3 Randomized Placebo-Controlled Trial Wei, Andrew H.; Montesinos, Pau; Ivanov, Vladimir; Dinardo, Courtney D., 0000-0001-9003-0390; Novak, Jan; Laribi, Kamel; Kim, Inho; Stevens, Don A.; Fiedler, Walter; Pagoni, Maria; Samoilova, Olga; Hu, Yu, 0000-0002-2815-4568; Anagnostopoulos, Achilles, 0000-0003-4384-9031; Bergeron, Julie; Hou, Jing-Zhou; Murthy, Vidhya; Yamauchi, Takahiro; Mcdonald, Andrew; Chyla, Brenda; Gopalakrishnan, Sathej; Jiang, Qi; Mendes, Wellington; Hayslip, John; Panayiotidis, Panayiotis, 0000-0003-0387-3993 Blood 2020
19946 10.1182/blood.2020006844 A Randomized Phase 3 Trial Of Zanubrutinib Vs Ibrutinib In Symptomatic Waldenstrom Macroglobulinemia: The Aspen Study Tam, Constantine S., 0000-0002-9759-5017; Opat, Stephen; D’Sa, Shirley; Jurczak, Wojciech, 0000-0003-1879-8084; Lee, Hui-Peng; Cull, Gavin; Owen, Roger G.; Marlton, Paula; Wahlin, Bjorn E.; Sanz, Ramon Garcia, 0000-0003-4120-2787; Mccarthy, Helen; Mulligan, Stephen; Tedeschi, Alessandra; Castillo, Jorge J.; Czyz, Jaroslaw, 0000-0001-9490-7532; Fernandez De Larrea, Carlos, 0000-0003-4930-9255; Belada, David; Libby, Edward; Matous, Jeffrey V.; Motta, Marina; Siddiqi, Tanya; Tani, Monica; Trneny, Marek, 0000-0002-6952-6073; Minnema, Monique C., 0000-0002-3139-8379; Buske, Christian; Leblond, Veronique; Trotman, Judith; Chan, Wai Y.; Schneider, Jingjing; Ro, Sunhee; Cohen, Aileen; Huang, Jane; Dimopoulos, Meletios Blood 2020
20006 10.1186/s12859-018-2585-4 Web-Based Design And Analysis Tools For Crispr Base Editing Hwang, Gue-Ho; Park, Jeongbin; Lim, Kayeong; Kim, Sunghyun; Yu, Jihyeon; Yu, Eunchong; Kim, Sang-Tae; Eils, Roland; Kim, Jin-Soo; Bae, Sangsu, 0000-0003-3615-8566 Bmc Bioinformatics 2018
20009 10.1186/s12870-018-1627-4 Crispr/Cas9-Mediated Slnpr1 Mutagenesis Reduces Tomato Plant Drought Tolerance Li, Rui; Liu, Chunxue; Zhao, Ruirui; Wang, Liu; Chen, Lin; Yu, Wenqing; Zhang, Shujuan; Sheng, Jiping; Shen, Lin, 0000-0002-7458-2133 Bmc Plant Biology 2019
20027 10.1186/s12915-019-0629-5 Application Of Crispr-Cas12A Temperature Sensitivity For Improved Genome Editing In Rice, Maize, And Arabidopsis Malzahn, Aimee A.; Tang, Xu; Lee, Keunsub; Ren, Qiurong; Sretenovic, Simon; Zhang, Yingxiao; Chen, Hongqiao; Kang, Minjeong; Bao, Yu; Zheng, Xuelian; Deng, Kejun; Zhang, Tao; Salcedo, Valeria; Wang, Kan; Zhang, Yong; Qi, Yiping, 0000-0002-9556-6706 Bmc Biology 2019
20216 10.1200/jco.18.00400 Cause Of Death In Follicular Lymphoma In The First Decade Of The Rituximab Era: A Pooled Analysis Of French And Us Cohorts Sarkozy, Clementine; Maurer, Matthew J.; Link, Brian K.; Ghesquieres, Herve; Nicolas, Emmanuelle; Thompson, Carrie A.; Traverse-Glehen, Alexandra; Feldman, Andrew L.; Allmer, Cristine; Slager, Susan L.; Ansell, Stephen M.; Habermann, Thomas M.; Bachy, Emmanuel; Cerhan, James R.; Salles, Gilles Journal Of Clinical Oncology 2019
20217 10.1200/jco.18.00605 First-Line Treatment Of Patients With Indolent Non-Hodgkin Lymphoma Or Mantle-Cell Lymphoma With Bendamustine Plus Rituximab Versus R-Chop Or R-Cvp: Results Of The Bright 5-Year Follow-Up Study Flinn, Ian W.; Van Der Jagt, Richard; Kahl, Brad; Wood, Peter; Hawkins, Tim; Macdonald, David; Simpson, David; Kolibaba, Kathryn; Issa, Samar; Chang, Julie; Trotman, Judith; Hallman, Doreen; Chen, Ling; Burke, John M. Journal Of Clinical Oncology 2019
20219 10.1200/jco.18.00915 Dynamo: A Phase Ii Study Of Duvelisib (Ipi-145) In Patients With Refractory Indolent Non-Hodgkin Lymphoma Flinn, Ian W.; Miller, Carole B.; Ardeshna, Kirit M.; Tetreault, Scott; Assouline, Sarit E.; Mayer, Jiri; Merli, Michele; Lunin, Scott D.; Pettitt, Andrew R.; Nagy, Zoltan; Tournilhac, Olivier; Abou-Nassar, Karem-Etienne; Crump, Michael; Jacobsen, Eric D.; De Vos, Sven; Kelly, Virginia M.; Shi, Weiliang; Steelman, Lori; Le, Ngocdiep; Weaver, David T.; Lustgarten, Stephanie; Wagner-Johnston, Nina D.; Zinzani, Pier Luigi Journal Of Clinical Oncology 2019
20225 10.1200/jco.18.01460 Final Results Of A Randomized, Phase Iii Study Of Rituximab With Or Without Idelalisib Followed By Open-Label Idelalisib In Patients With Relapsed Chronic Lymphocytic Leukemia Journal Of Clinical Oncology 2019
20229 10.1200/jco.18.01580 Fixed Duration Of Venetoclax-Rituximab In Relapsed/Refractory Chronic Lymphocytic Leukemia Eradicates Minimal Residual Disease And Prolongs Survival: Post-Treatment Follow-Up Of The Murano Phase Iii Study Kater, Arnon P.; Seymour, John F.; Hillmen, Peter; Eichhorst, Barbara; Langerak, Anton W.; Owen, Carolyn; Verdugo, Maria; Wu, Jenny; Punnoose, Elizabeth A.; Jiang, Yanwen; Wang, Jue; Boyer, Michelle; Humphrey, Kathryn; Mobasher, Mehrdad; Kipps, Thomas J. Journal Of Clinical Oncology 2019
20232 10.1200/jco.18.01600 Venetoclax Combined With Low-Dose Cytarabine For Previously Untreated Patients With Acute Myeloid Leukemia: Results From A Phase Ib/Ii Study Wei, Andrew H.; Strickland, Stephen A.; Hou, Jing-Zhou; Fiedler, Walter; Lin, Tara L.; Walter, Roland B.; Enjeti, Anoop; Tiong, Ing Soo; Savona, Michael; Lee, Sangmin; Chyla, Brenda; Popovic, Relja; Salem, Ahmed Hamed; Agarwal, Suresh; Xu, Tu; Fakouhi, Kaffa M.; Humerickhouse, Rod; Hong, Wan-Jen; Hayslip, John; Roboz, Gail J. Journal Of Clinical Oncology 2019
20239 10.1200/jco.19.00010 Augment: A Phase Iii Study Of Lenalidomide Plus Rituximab Versus Placebo Plus Rituximab In Relapsed Or Refractory Indolent Lymphoma Leonard, John P.; Trneny, Marek; Izutsu, Koji; Fowler, Nathan H.; Hong, Xiaonan; Zhu, Jun; Zhang, Huilai; Offner, Fritz; Scheliga, Adriana; Nowakowski, Grzegorz S.; Pinto, Antonio; Re, Francesca; Fogliatto, Laura Maria; Scheinberg, Phillip; Flinn, Ian W.; Moreira, Claudia; Cabecadas, Jose; Liu, David; Kalambakas, Stacey; Fustier, Pierre; Wu, Chengqing; Gribben, John G. Journal Of Clinical Oncology 2019
20253 10.1200/jco.19.00894 Ibrutinib Plus Venetoclax In Relapsed/Refractory Chronic Lymphocytic Leukemia: The Clarity Study Hillmen, Peter; Rawstron, Andy C.; Brock, Kristian; Munoz-Vicente, Samuel; Yates, Francesca J.; Bishop, Rebecca; Boucher, Rebecca; Macdonald, Donald; Fegan, Christopher; Mccaig, Alison; Schuh, Anna; Pettitt, Andrew; Gribben, John G.; Patten, Piers E.M.; Devereux, Stephen; Bloor, Adrian; Fox, Christopher P.; Forconi, Francesco; Munir, Talha Journal Of Clinical Oncology 2019
20256 10.1200/jco.19.01073 Sustained Progression-Free Survival Benefit Of Rituximab Maintenance In Patients With Follicular Lymphoma: Long-Term Results Of The Prima Study Bachy, Emmanuel; Seymour, John F.; Feugier, Pierre; Offner, Fritz; Lopez-Guillermo, Armando; Belada, David; Xerri, Luc; Catalano, John V.; Brice, Pauline; Lemonnier, Francois; Martin, Alejandro; Casasnovas, Olivier; Pedersen, Lars M.; Dorvaux, Veronique; Simpson, David; Leppa, Sirpa; Gabarre, Jean; Da Silva, Maria G.; Glaisner, Sylvie; Ysebaert, Loic; Vekhoff, Anne; Intragumtornchai, Tanin; Le Gouill, Steven; Lister, Andrew; Estell, Jane A.; Milone, Gustavo; Sonet, Anne; Farhi, Jonathan; Zeuner, Harald; Tilly, Herve; Salles, Gilles Journal Of Clinical Oncology 2019
20281 10.1200/jco.19.03011 Impact Of Conditioning Intensity Of Allogeneic Transplantation For Acute Myeloid Leukemia With Genomic Evidence Of Residual Disease Hourigan, Christopher S.; Dillon, Laura W.; Gui, Gege; Logan, Brent R.; Fei, Mingwei; Ghannam, Jack; Li, Yuesheng; Licon, Abel; Alyea, Edwin P.; Bashey, Asad; Deeg, H. Joachim; Devine, Steven M.; Fernandez, Hugo F.; Giralt, Sergio; Hamadani, Mehdi; Howard, Alan; Maziarz, Richard T.; Porter, David L.; Scott, Bart L.; Warlick, Erica D.; Pasquini, Marcelo C.; Horwitz, Mitchell E. Journal Of Clinical Oncology 2020
20284 10.1200/jco.19.03345 Sorafenib Maintenance After Allogeneic Hematopoietic Stem Cell Transplantation For Acute Myeloid Leukemia With Flt3<U+2013>Internal Tandem Duplication Mutation (Sormain) Burchert, Andreas; Bug, Gesine; Fritz, Lea V.; Finke, Jurgen; Stelljes, Matthias; Rollig, Christoph; Wollmer, Ellen; Wasch, Ralph; Bornhauser, Martin; Berg, Tobias; Lang, Fabian; Ehninger, Gerhard; Serve, Hubert; Zeiser, Robert; Wagner, Eva-Maria; Kroger, Nicolaus; Wolschke, Christine; Schleuning, Michael; Gotze, Katharina S.; Schmid, Christoph; Crysandt, Martina; Eseling, Eva; Wolf, Dominik; Wang, Ying; Bohm, Alexandra; Thiede, Christian; Haferlach, Torsten; Michel, Christian; Bethge, Wolfgang; Wundisch, Thomas; Brandts, Christian; Harnisch, Susanne; Wittenberg, Michael; Hoeffkes, Heinz-Gert; Rospleszcz, Susanne; Burchardt, Alexander; Neubauer, Andreas; Brugger, Markus; Strauch, Konstantin; Schade-Brittinger, Carmen; Metzelder, Stephan K. Journal Of Clinical Oncology 2020
20285 10.1200/jco.19.03355 Ascend: Phase Iii, Randomized Trial Of Acalabrutinib Versus Idelalisib Plus Rituximab Or Bendamustine Plus Rituximab In Relapsed Or Refractory Chronic Lymphocytic Leukemia Ghia, Paolo; Pluta, Andrzej; Wach, Malgorzata; Lysak, Daniel; Kozak, Tomas; Simkovic, Martin; Kaplan, Polina; Kraychok, Iryna; Illes, Arpad; De La Serna, Javier; Dolan, Sean; Campbell, Phillip; Musuraca, Gerardo; Jacob, Abraham; Avery, Eric; Lee, Jae Hoon; Liang, Wei; Patel, Priti; Quah, Cheng; Jurczak, Wojciech Journal Of Clinical Oncology 2020
20308 10.1200/jco.2017.76.6840 Venetoclax For Patients With Chronic Lymphocytic Leukemia With 17P Deletion: Results From The Full Population Of A Phase Ii Pivotal Trial Stilgenbauer, Stephan; Eichhorst, Barbara; Schetelig, Johannes; Hillmen, Peter; Seymour, John F.; Coutre, Steven; Jurczak, Wojciech; Mulligan, Stephen P.; Schuh, Anna; Assouline, Sarit; Wendtner, Clemens-Martin; Roberts, Andrew W.; Davids, Matthew S.; Bloehdorn, Johannes; Munir, Talha; Bottcher, Sebastian; Zhou, Lang; Salem, Ahmed Hamed; Desai, Monali; Chyla, Brenda; Arzt, Jennifer; Kim, Su Young; Verdugo, Maria; Gordon, Gary; Hallek, Michael; Wierda, William G. Journal Of Clinical Oncology 2018
20311 10.1200/jco.2017.77.6112 Cpx-351 (Cytarabine And Daunorubicin) Liposome For Injection Versus Conventional Cytarabine Plus Daunorubicin In Older Patients With Newly Diagnosed Secondary Acute Myeloid Leukemia Lancet, Jeffrey E.; Uy, Geoffrey L.; Cortes, Jorge E.; Newell, Laura F.; Lin, Tara L.; Ritchie, Ellen K.; Stuart, Robert K.; Strickland, Stephen A.; Hogge, Donna; Solomon, Scott R.; Stone, Richard M.; Bixby, Dale L.; Kolitz, Jonathan E.; Schiller, Gary J.; Wieduwilt, Matthew J.; Ryan, Daniel H.; Hoering, Antje; Banerjee, Kamalika; Chiarella, Michael; Louie, Arthur C.; Medeiros, Bruno C. Journal Of Clinical Oncology 2018
20943 10.3324/haematol.2018.188888 Gemtuzumab Ozogamicin For De Novo Acute Myeloid Leukemia: Final Efficacy And Safety Updates From The Open-Label, Phase Iii Alfa-0701 Trial Lambert, Juliette; Pautas, Cecile; Terre, Christine; Raffoux, Emmanuel; Turlure, Pascal; Caillot, Denis; Legrand, Ollivier; Thomas, Xavier; Gardin, Claude; Gogat-Marchant, Karin; Rubin, Stephen D.; Benner, Rebecca J.; Bousset, Pierre; Preudhomme, Claude; Chevret, Sylvie; Dombret, Herve; Castaigne, Sylvie Haematologica 2018
20947 10.3324/haematol.2019.222588 Venetoclax Resistance And Acquired Bcl2 Mutations In Chronic Lymphocytic Leukemia Tausch, Eugen; Close, William; Dolnik, Anna; Bloehdorn, Johannes; Chyla, Brenda; Bullinger, Lars; Dohner, Hartmut; Mertens, Daniel; Stilgenbauer, Stephan Haematologica 2019
21013 10.3389/fonc.2019.01380 Therapeutic Targeting Of The Macrophage Immune Checkpoint Cd47 In Myeloid Malignancies Chao, Mark P.; Takimoto, Chris H.; Feng, Dong Dong; Mckenna, Kelly; Gip, Phung; Liu, Jie; Volkmer, Jens-Peter; Weissman, Irving L.; Majeti, Ravindra Frontiers In Oncology 2020
21176 10.3390/ijms20020402 Transgene-Free Genome Editing In Tomato And Potato Plants Using Agrobacterium-Mediated Delivery Of A Crispr/Cas9 Cytidine Base Editor Veillet, Florian; Perrot, Laura; Chauvin, Laura; Kermarrec, Marie-Paule; Guyon-Debast, Anouchka; Chauvin, Jean-Eric; Nogue, Fabien; Mazier, Marianne, 0000-0002-1441-6897 International Journal Of Molecular Sciences 2019